Outcome of haematopoietic cell transplantation in children with lysosomal acid lipase deficiency: a study on behalf of the EBMT Inborn Errors Working Party

被引：4

作者：

Lum, Su Han ^{[1
,2
]}

Minkov, Milen ^{[3
]}

Jones, Simon A. ^{[4
]}

Hazelaar, Sheree ^{[5
]}

Sirait, Tiarlan ^{[5
]}

Potter, Jane E. ^{[6
]}

Stepensky, Polina ^{[7
]}

Garban, Frederic ^{[8
]}

Pichler, Herbert ^{[9
]}

Stein, Jerry ^{[10
]}

Kaya, Zuhre ^{[11
]}

Schulz, Ansgar ^{[12
]}

Mellgren, Karin ^{[13
]}

de Heredia, Cristina Diaz ^{[14
]}

Pochon, Cecile ^{[15
]}

Riesco, Susana ^{[16
]}

Diaz, Miguel Angel ^{[17
]}

Michel, Gerard ^{[18
,19
]}

Lindemans, Caroline ^{[20
,21
]}

Gruhn, Bernd ^{[22
]}

Albert, Michael H. ^{[23
]}

Lankester, Arjan C. ^{[24
]}

Neven, Benedicte

Wynn, Robert ^{[6
]}

机构：

[1] Great North Childrens Hosp, Childrens Hematopoiet Stem Cell Transplant Unit, Newcastle Upon Tyne, England

[2] Newcastle Univ, Translat & Clin Res Inst, Newcastle Upon Tyne, England

[3] Sigmund Freud Univ, Vienna, Austria

[4] St Marys Hosp, Willink Unit, Manchester, England

[5] EBMT Leiden Study Unit, Leiden, Netherlands

[6] Royal Manchester Childrens Hosp, Manchester, England

[7] Hebrew Univ Jerusalem, Hadassah Hosp, Fac Med, Dept Bone Marrow Transplantat, Jerusalem, Israel

[8] Univ Grenoble Alpes, CHU Grenoble Alpes, Grenoble, France

[9] Med Univ Vienna, St Anna Childrens Hosp, Dept Paediat, Vienna, Austria

[10] Schneider Childrens Med Ctr Israel, Assistance Publ Hop Paris APHP, Pediat Hematol Immunol & Rheumatol Unit, Petah Tiqwa, Israel

[11] Gazi Univ, Unit Pediat Hematol & Pediat BMT, Sch Med, Ankara, Turkiye

[12] Univ Med Ctr Ulm, Dept Pediat, Ulm, Germany

[13] Sahlgrens Univ Hosp, Dept Pediat Oncol, Gothenburg, Sweden

[14] Hosp Univ Vall Hebron, Dept Pediat Hematol & Oncol, Barcelona, Spain

[15] Univ Lorraine, Nancy Univ Hosp, Pediat Onco Hematol Dept, Nancy, France

[16] Hosp Univ Salamanca, Dept Pediat, Salamanca, Spain

[17] Nino Jesus Childrens Hosp, Madrid, Spain

[18] La Timone Childrens Hosp, Marseille, France

[19] Aix Marseille Univ, Marseille, France

[20] Univ Med Ctr, Dept Pediat, Utrecht, Netherlands

[21] Princess Maxima Ctr Pediat Oncol, Utrecht, Netherlands

[22] Jena Univ Hosp, Dept Pediat, Jena, Germany

[23] Ludwig Maximilians Univ Munchen, Dr von Hauner Univ Childrens Hosp, Munich, Germany

[24] Leiden Univ, Willem Alexander Childrens Hosp, Pediat Stem Cell Transplantat program, Med Ctr, Leiden, Netherlands

来源：

BONE MARROW TRANSPLANTATION | 2023年 / 58卷 / 05期

关键词：

WOLMANS-DISEASE;

D O I：

10.1038/s41409-023-01918-4

中图分类号：

Q6 [生物物理学];

学科分类号：

071011 ;

摘要：

引用

页码：594 / 596

页数：3

共 50 条

[31] Allogeneic hematopoietic cell transplantation for myelodysplastic syndrome unclassifiable - a retrospective study on behalf of the Chronic Malignancies Working Party of the EBMT
Drozd-Sokolowska, Joanna
Gras, Luuk
Zinger, Nienke
Zahrani, Mohsen Al
Passweg, Jakob
Byrne, Jenny
Ho, Aloysius
Huang, Xiao-jun
Kroeger, Nicolaus
Mayer, Jiri
Russo, Domenico
De Becker, Ann
Tbakhi, Abdelghani
Stamatoullas, Aspasia
Valerius, Thomas
Hayden, Patrick
McLornan, Donal P.
Onida, Francesco
Scheid, Christof
Robin, Marie
Yakoub-Agha, Ibrahim
BONE MARROW TRANSPLANTATION, 2023, 58 (02) : 222 - 225
[32] Allogeneic hematopoietic cell transplantation for myelodysplastic syndrome unclassifiable – a retrospective study on behalf of the Chronic Malignancies Working Party of the EBMT
Joanna Drozd-Sokolowska
Luuk Gras
Nienke Zinger
Mohsen Al Zahrani
Jakob Passweg
Jenny Byrne
Aloysius Ho
Xiao-jun Huang
Nicolaus Kröger
Jiri Mayer
Domenico Russo
Ann De Becker
Abdelghani Tbakhi
Aspasia Stamatoullas
Thomas Valerius
Patrick Hayden
Donal P. McLornan
Francesco Onida
Christof Scheid
Marie Robin
Ibrahim Yakoub-Agha
Bone Marrow Transplantation, 2023, 58 : 222 - 225
[33] Allogeneic haematopoietic cell transplantation for therapy-related myeloid neoplasms arising following treatment for lymphoma: a retrospective study on behalf of the Chronic Malignancies Working Party of the EBMT
Mitja Nabergoj
Diderik-Jan Eikema
Linda Koster
Uwe Platzbecker
Katja Sockel
Jürgen Finke
Nicolaus Kröger
Edouard Forcade
Arnon Nagler
Matthias Eder
Johanna Tischer
Annoek E. C. Broers
Jürgen Kuball
Keith M. O. Wilson
Mathilde Hunault-Berger
Matthew Collin
Domenico Russo
Lucía López Corral
Grzegorz Helbig
Alberto Mussetti
Christof Scheid
Carmelo Gurnari
Kavita Raj
Joanna Drozd-Sokolowska
Ibrahim Yakoub-Agha
Marie Robin
Donal P. McLornan
Bone Marrow Transplantation, 2024, 59 : 395 - 402
[34] Solid organ transplantation (SOT) after haematopoietic stem cell transplantation (HSCT) in pediatric patients. a multicentric retrospective EBMT study; on behalf of Paediatric Disease Working Party (PDWP)
Faraci, M.
Dalissier, A.
Bertaina, A.
Lanino, E.
Ifversen, M. R. S.
Schulz, A.
Gennery, A.
Burkhardt, B.
Serra, I. B.
Diaz-de-Heredia, C.
Lankester, A.
Gruhn, B.
Matthes-Martin, S.
Kuehl, J-S
Varotto, S.
Paillard, C.
Guilmatre, A.
Sastre, A.
Abecasis, M.
Garwer, B.
Sedlacek, P.
Boelens, J. J.
Bader, P.
BONE MARROW TRANSPLANTATION, 2017, 52 : S106 - S107
[35] Allogeneic haematopoietic cell transplantation for therapy-related myeloid neoplasms arising following treatment for lymphoma: a retrospective study on behalf of the Chronic Malignancies Working Party of the EBMT
Nabergoj, Mitja
Eikema, Diderik-Jan
Koster, Linda
Platzbecker, Uwe
Sockel, Katja
Finke, Juergen
Kroeger, Nicolaus
Forcade, Edouard
Nagler, Arnon
Eder, Matthias
Tischer, Johanna
Broers, Annoek E. C.
Kuball, Juergen
Wilson, Keith M. O.
Hunault-Berger, Mathilde
Collin, Matthew
Russo, Domenico
Corral, Lucia Lopez
Helbig, Grzegorz
Mussetti, Alberto
Scheid, Christof
Gurnari, Carmelo
Raj, Kavita
Drozd-Sokolowska, Joanna
Yakoub-Agha, Ibrahim
Robin, Marie
Mclornan, Donal P.
BONE MARROW TRANSPLANTATION, 2024, 59 (03) : 395 - 402
[36] Outcomes of cord blood transplantation for Hurler syndrome. A eurocord-working party inborn errors EBMT survey
Boelens, J. J.
Bierings, M.
Wynn, R.
O'Mearra, A.
Veys, P.
Bertrand, Y.
Fischer, A.
Cavazzana-Calvo, M.
Wulffraat, N.
Gluckman, E.
Rocha, V.
BONE MARROW TRANSPLANTATION, 2007, 39 : S36 - S37
[37] Haematopoietic stem cell transplantation in children with inborn errors of immunity: A single centre experience
Bilir, Ozlem Arman
Karaatmaca, Betul
Bozkaya, Ikbal Ok
Kanbur, Serife Mehtap
Kacar, Dilek
Metin, Ayse
Ozbek, Namik Yasar
SCANDINAVIAN JOURNAL OF IMMUNOLOGY, 2025, 101 (01)
[38] Results of Unrelated Donor Hematopoietic Stem Cell Transplantation for Sickle Cell Disease in Europe on Behalf of Paediatric Diseases (PDWP) and Inborn Errors Working Parties (IEWP) of the EBMT
Gluckman, Eliane
de la Fuente, Josu
Cappelli, Barbara
Scigliuolo, Graziana M.
Volt, Fernanda
Tozatto-Maio, Karina
Rocha, Vanderson
Mina, Tommaso
O'Boyle, Farah
Smiers, Frans
Da Cunha-Riehm, Claudia Bettoni
Calore, Elisabetta
Bonanomi, Sonia
Graphakos, Stelios
Paisiou, Anna
Albert, Michael H.
Ruggeri, Annalisa
Zecca, Marco
Lankester, Arjan C.
Corbacioglu, Selim
BLOOD, 2019, 134
[39] Outcome of Myeloablative and Reduced-intensity conditioned Allogeneic Haematopoietic Stem Cell Transplantation in Myelofibrosis: A Retrospective Study by the Chronic Malignancies Working Party of the EBMT
McLornan, Donal
Szydlo, Richard
Robin, Marie
van Biezen, Anja
Koster, Linda
Blok, Henrik Jan P.
Beelen, Dietrich
Brecht, Arne
Socie, Gerard
Ehninger, Gerhard
Van Lint, Maria Teresa
Niederwieser, Dietger
Arnold, Renate
Finke, Jurgen
Vitek, Antonin
Yakoub-Agha, Ibrahim
Volin, Liisa
Dreger, Peter
Kanz, Lothar
Petersen, Eefke
Chevallier, Patrice
Stelljes, Matthias
Robinson, Stephen
Klyuchnikov, E.
Chalandon, Yves
Kroger, Nicolaus
BONE MARROW TRANSPLANTATION, 2018, 53 : 47 - 49
[40] Onset and outcome of pregnancy after autologous haematopoietic stem cell transplantation (AHSCT) for autoimmune diseases: a retrospective study of the EBMT Autoimmune Disease Working Party
Snarski, E.
Badoglio, M.
Moore, J.
Tan, J.
Rovira, M.
Saiz, A.
Musso, M.
Martin, T.
Snowden, J.
Forge, D.
BONE MARROW TRANSPLANTATION, 2013, 48 : S377 - S377

← 1 2 3 4 5 →