ABO-503, a Novel Gene Therapy for Treatment of X-Linked Retinoschisis

被引:0
|
作者
Fogerty, Joseph [1 ]
Wille, Paul T. [1 ]
Padegimas, Linas [2 ]
Kevany, Brian M. [1 ]
机构
[1] Abeona Therapeut, Cleveland, OH USA
[2] Forge Biol, Grove City, OH USA
关键词
D O I
暂无
中图分类号
Q81 [生物工程学(生物技术)]; Q93 [微生物学];
学科分类号
071005 ; 0836 ; 090102 ; 100705 ;
摘要
1131
引用
收藏
页码:542 / 542
页数:1
相关论文
共 50 条
  • [22] X-linked juvenile retinoschisis: mutations at the retinoschisis and Norrie disease gene loci?
    Hiraoka, M
    Rossi, F
    Trese, MT
    Shastry, BS
    JOURNAL OF HUMAN GENETICS, 2001, 46 (02) : 53 - 56
  • [23] X-linked juvenile retinoschisis
    Errera, M. H.
    Kohly, R. P.
    Webster, A. R.
    JOURNAL FRANCAIS D OPHTALMOLOGIE, 2011, 34 (09): : 678 - 678
  • [24] X-LINKED CONGENITAL RETINOSCHISIS
    KELLNER, U
    BRUMMER, S
    FOERSTER, MH
    WESSING, A
    GRAEFES ARCHIVE FOR CLINICAL AND EXPERIMENTAL OPHTHALMOLOGY, 1990, 228 (05) : 432 - 437
  • [25] X-LINKED RETINOSCHISIS AND LINKAGE
    GAL, A
    CLINICAL GENETICS, 1988, 33 (02) : 143 - 143
  • [26] X-LINKED JUVENILE RETINOSCHISIS
    MCMAHON, TT
    ROSENTHAL, BP
    JOURNAL OF THE AMERICAN OPTOMETRIC ASSOCIATION, 1983, 54 (01) : 55 - 61
  • [27] X-linked retinoschisis: an update
    Sikkink, Stephen K.
    Biswas, Susmito
    Parry, Neil R. A.
    Stanga, Paulo E.
    Trump, Dorothy
    JOURNAL OF MEDICAL GENETICS, 2007, 44 (04) : 225 - 232
  • [28] Exclusion of PPEF as the gene causing X-linked juvenile retinoschisis
    E. van de Vosse
    Brunella Franco
    P. van der Bent
    Eugenio Montini
    Ulrike Orth
    Andre Hanauer
    N. Tijmes
    G.-J. B. van Ommen
    Andrea Ballabio
    J. T. den Dunnen
    Arthur A. B. Bergen
    Human Genetics, 1997, 101 : 235 - 237
  • [29] REFINEMENT OF THE CHROMOSOMAL POSITION OF THE X-LINKED JUVENILE RETINOSCHISIS GENE
    BERGEN, AAB
    TENBRINK, JB
    BLEEKERWAGEMAKERS, LM
    VANSCHOONEVELD, MJ
    JOURNAL OF MEDICAL GENETICS, 1994, 31 (12) : 972 - 975
  • [30] Positional cloning of the gene associated with X-linked juvenile retinoschisis
    Christian G. Sauer
    Andrea Gehrig
    Regina Warneke-Wittstock
    Andreas Marquardt
    Cecil C. Ewing
    Alice Gibson
    Birgit Lorenz
    Bernhard Jurklies
    Bernhard H.F. Weber
    Nature Genetics, 1997, 17 : 164 - 170