Impact Of Patisiran On Health Status And Quality Of Life In Patients With Transthyretin Cardiac Amyloidosis

被引:0
|
作者
Shah, Zubair [1 ]
Obici, Laura [2 ]
Kale, Parag [3 ]
Mitter, Sumeet S. [4 ]
Eldhagen, Per [5 ]
Hashimoto, Toru [6 ]
Correia, Edileide De Barros [7 ]
White, Matthew T. [8 ]
Bender, Sean [8 ]
Jay, Patrick Y. [8 ]
Capocelli, Kelley [8 ]
Hanna, Mazen A. [9 ]
机构
[1] Univ Kansas, Med Ctr, Kansas City, KS USA
[2] Fdn IRCCS Policlin San Matteo Pavia, Pavia, Italy
[3] Baylor Univ, Med Ctr, Dallas, TX USA
[4] Icahn Sch Med Mt Sinai, New York, NY USA
[5] Karolinska Univ Hosp, Stockholm, Sweden
[6] Kyushu Univ Hosp, Fukuoka, Japan
[7] Inst Dante Pazzanese Cardiol, Sao Paulo, Brazil
[8] Alnylam Pharmaceut, Cambridge, MA USA
[9] Cleveland Clin Fdn, Cleveland, OH USA
关键词
D O I
暂无
中图分类号
R5 [内科学];
学科分类号
1002 ; 100201 ;
摘要
030
引用
收藏
页码:134 / 134
页数:1
相关论文
共 50 条
  • [1] Patisiran in Patients with Transthyretin Cardiac Amyloidosis
    Martinez-Selles, Manuel
    [J]. NEW ENGLAND JOURNAL OF MEDICINE, 2024, 390 (03): : 286 - 287
  • [2] Patisiran Treatment in Patients with Transthyretin Cardiac Amyloidosis
    Maurer, Mathew S.
    Kale, Parag
    Fontana, Marianna
    Berk, John L.
    Grogan, Martha
    Gustafsson, Finn
    Hung, Rebecca R.
    Gottlieb, Robert L.
    Damy, Thibaud
    Gonzalez-Duarte, Alejandra
    Sarswat, Nitasha
    Sekijima, Yoshiki
    Tahara, Nobuhiro
    Taylor, Mark S.
    Kubanek, Milos
    Donal, Erwan
    Palecek, Tomas
    Tsujita, Kenichi
    Tang, W. H. Wilson
    Yu, Wen-Chung
    Obici, Laura
    Simoes, Marcus
    Fernandes, Fabio
    Poulsen, Steen Hvitfeldt
    Diemberger, Igor
    Perfetto, Federico
    Solomon, Scott D.
    Di Carli, Marcelo
    Badri, Prajakta
    White, Matthew T.
    Chen, Jihong
    Yureneva, Elena
    Sweetser, Marianne T.
    Jay, Patrick Y.
    Garg, Pushkal P.
    Vest, John
    Gillmore, Julian D.
    APOLLO-B Trial Investigators
    [J]. NEW ENGLAND JOURNAL OF MEDICINE, 2023, 389 (17): : 1553 - 1565
  • [3] Patisiran improves quality of life in patients with ATTR cardiac amyloidosis
    Forte, Elvira
    [J]. NATURE CARDIOVASCULAR RESEARCH, 2023, 2 (12): : 1101 - 1101
  • [4] Patisiran improves quality of life in patients with ATTR cardiac amyloidosis
    Elvira Forte
    [J]. Nature Cardiovascular Research, 2023, 2 : 1101 - 1101
  • [5] Impact of Patisiran, an investigational RNAi Therapeutic, on nutritional status in patients with hereditary Transthyretin-Mediated Amyloidosis
    Obici, L.
    Coelho, T.
    Adams, D.
    Gonzalez-Duarte, A.
    O'Riordan, W.
    Yang, C-C.
    Yamashita, T.
    Kristen, A.
    Tournev, I.
    Schmidt, H.
    Berk, J.
    Lin, K-P.
    Gandhi, P.
    Sweetser, M.
    Chen, J.
    Goyal, S.
    Gollob, J.
    Suhr, O.
    [J]. EUROPEAN JOURNAL OF NEUROLOGY, 2018, 25 : 17 - 17
  • [6] Baseline Characteristics Of Patients With Transthyretin Cardiac Amyloidosis Enrolled In The Patisiran Expanded Access Program
    Saha, Naveen
    Shah, Zubair
    Hanna, Mazen A.
    Nikolova, Andriana
    Moffitt, Colleen
    Summers, Catherine
    Capocelli, Kelley
    Drachman, Brian M.
    [J]. JOURNAL OF CARDIAC FAILURE, 2024, 30 (01) : 156 - 156
  • [7] Italian Real-Life Experience of Patients with Hereditary Transthyretin Amyloidosis Treated with Patisiran
    Di Stefano, Vincenzo
    Fava, Antonella
    Gentile, Luca
    Guaraldi, Pietro
    Leonardi, Luca
    Poli, Loris
    Tagliapietra, Matteo
    Vastola, Michele
    Fanara, Salvatore
    Ferrero, Bruno
    Giorgi, Mauro
    Perfetto, Federico
    Russo, Massimo
    Russo, Domitilla
    [J]. PHARMACOGENOMICS & PERSONALIZED MEDICINE, 2022, 15 : 499 - 514
  • [8] Impact of Patisiran, an RNAi Therapeutic, on Diarrhea Symptoms in Patients With Hereditary Transthyretin-Mediated Amyloidosis
    Obici, Laura
    Gonzalez-Duarte, Alejandra
    Waddington-Cruz, Marcia
    Lin, Hollis
    Merkel, Madeline
    Wang, Yue
    Ueda, Mitsuharu
    [J]. AMERICAN JOURNAL OF GASTROENTEROLOGY, 2020, 115 : S1657 - S1657
  • [9] Natural History, Quality of Life, and Outcome in Cardiac Transthyretin Amyloidosis
    Lane, Thirusha
    Fontana, Marianna
    Martinez-Naharro, Ana
    Quarta, Candida Cristina
    Whelan, Carol J.
    Petrie, Aviva
    Rowczenio, Dorota M.
    Gilbertson, Janet A.
    Hutt, David F.
    Rezk, Tamer
    Strehina, Svetla G.
    Caringal-Galima, Joan
    Manwani, Richa
    Sharpley, Faye A.
    Wechalekar, Ashutosh D.
    Lachmann, Helen J.
    Mahmood, Shameem
    Sachchithanantham, Sajitha
    Drage, Edmund P. S.
    Jenner, Harvey D.
    McDonald, Rosie
    Bertolli, Ottavia
    Calleja, Alan
    Hawkins, Philip N.
    Gillmore, Julian D.
    [J]. CIRCULATION, 2019, 140 (01) : 16 - 26
  • [10] Impact of Patisiran, an RNAi Therapeutic, on Orthostatic Intolerance in Patients with Hereditary Transthyretin-Mediated Amyloidosis
    Gonzalez-Duarte, Alejandra
    Judge, Daniel P.
    Dispenzieri, Angela
    Lin, Hollis
    Merkel, Madeline
    Wang, Yue
    Polydefkis, Michael
    [J]. NEUROLOGY, 2020, 94 (15)