Impact of Patisiran, an RNAi Therapeutic, on Diarrhea Symptoms in Patients With Hereditary Transthyretin-Mediated Amyloidosis

被引:0
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作者
Obici, Laura [1 ]
Gonzalez-Duarte, Alejandra [2 ]
Waddington-Cruz, Marcia [3 ]
Lin, Hollis [4 ]
Merkel, Madeline [4 ]
Wang, Yue [4 ]
Ueda, Mitsuharu [5 ]
机构
[1] Fdn IRCCS Policlinco San Matteo, Pavia, Lombardia, Italy
[2] Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, Tlaxcala, Mexico
[3] Hosp Univ Clementino Fraga Filho, Rio De Janeiro, Brazil
[4] Alnylam Pharmaceut, Cambridge, MA USA
[5] Kumamoto Univ Hosp, Kumamoto, Kumamoto, Japan
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暂无
中图分类号
R57 [消化系及腹部疾病];
学科分类号
摘要
S3155
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页码:S1657 / S1657
页数:1
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