Optimizing Therapeutic Base Editing for Hereditary Tyrosinemia Type 1

被引：0

作者：

Dumitru, Ana Maria ^{[1
]}

Berkowitz, Cara ^{[1
]}

Whittaker, Madelynn ^{[2
]}

Wang, Xiao ^{[3
]}

Kus, Nicole ^{[1
]}

Luks, Valerie ^{[1
]}

Riley, John ^{[1
]}

Carpenter, Marco ^{[1
]}

Archer, Nicholas F. ^{[4
]}

Brooks, Dominique ^{[3
]}

Johnston, William ^{[1
]}

Alameh, Mohamad Gabriel ^{[5
]}

Musunuru, Kiran ^{[2
]}

Peranteau, William ^{[1
]}

机构：

[1] Childrens Hosp Philadelphia, Philadelphia, PA USA

[2] Univ Penn, Philadelphia, PA USA

[3] Univ Penn, Cardiovasc Inst, Perelman Sch Med, Philadelphia, PA USA

[4] Drexel Univ, Coll Med, Philadelphia, PA USA

[5] Univ Penn, Engn mRNA & Targeted Nanomed Core, Philadelphia, PA USA

来源：

MOLECULAR THERAPY | 2023年 / 31卷 / 04期

关键词：

D O I：

暂无

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

153

引用

页码：83 / 84

页数：2

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