Optimizing Therapeutic Base Editing for Hereditary Tyrosinemia Type 1

被引：0
|
作者：
Dumitru, Ana Maria [1 ]
Berkowitz, Cara [1 ]
Whittaker, Madelynn [2 ]
Wang, Xiao [3 ]
Kus, Nicole [1 ]
Luks, Valerie [1 ]
Riley, John [1 ]
Carpenter, Marco [1 ]
Archer, Nicholas F. [4 ]
Brooks, Dominique [3 ]
Johnston, William [1 ]
Alameh, Mohamad Gabriel [5 ]
Musunuru, Kiran [2 ]
Peranteau, William [1 ]
机构：
[1] Childrens Hosp Philadelphia, Philadelphia, PA USA
[2] Univ Penn, Philadelphia, PA USA
[3] Univ Penn, Cardiovasc Inst, Perelman Sch Med, Philadelphia, PA USA
[4] Drexel Univ, Coll Med, Philadelphia, PA USA
[5] Univ Penn, Engn mRNA & Targeted Nanomed Core, Philadelphia, PA USA
来源：
MOLECULAR THERAPY | 2023年 / 31卷 / 04期
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
153
引用
收藏
页码：83 / 84
页数：2
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