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- [31] HELIOS-A: 9-month results from the phase 3 study of vutrisiran in patients with hereditary transthyretin-mediated amyloidosis with polyneuropathyJOURNAL OF THE NEUROLOGICAL SCIENCES, 2021, 429Adams, Davide论文数: 0 引用数: 0 h-index: 0机构: Univ Paris Saclay, INSERM, U1195, Dept Neurol, Paris, France Univ Paris Saclay, INSERM, U1195, Dept Neurol, Paris, FranceTournev, Ivailo论文数: 0 引用数: 0 h-index: 0机构: Univ Hosp Aleksandrovska, Dept Neurol, Clin Nervous Dis, Sofia, Bulgaria Univ Paris Saclay, INSERM, U1195, Dept Neurol, Paris, FranceTaylor, Mark论文数: 0 引用数: 0 h-index: 0机构: Univ Sydney, Westmead Hosp, Dept Clin Immunol & Allergy, Sydney, NSW, Australia Univ Sydney, Westmead Clin Sch, Dept Clin Immunol & Allergy, Sydney, NSW, Australia Univ Paris Saclay, INSERM, U1195, Dept Neurol, Paris, FranceCoelho, Teresa论文数: 0 引用数: 0 h-index: 0机构: Ctr Hosp Univ Porto, Dept Neurosci, Sydney, NSW, Australia Univ Paris Saclay, INSERM, U1195, Dept Neurol, Paris, FrancePlante-Bordeneuve, Violaine论文数: 0 引用数: 0 h-index: 0机构: Univ Paris Est, CHU Henri Mondor, AP HP, INSERM,U955,Team 10,Neurol Dept, Creteil, France Univ Paris Saclay, INSERM, U1195, Dept Neurol, Paris, FranceBerk, John论文数: 0 引用数: 0 h-index: 0机构: Boston Med Ctr, Dept Med, Boston, MA USA Univ Paris Saclay, INSERM, U1195, Dept Neurol, Paris, FranceGonzalez-Duarte, Alejandra论文数: 0 引用数: 0 h-index: 0机构: Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Dept Neurol, Mexico City, DF, Mexico Univ Paris Saclay, INSERM, U1195, Dept Neurol, Paris, FranceGillmore, Julian论文数: 0 引用数: 0 h-index: 0机构: UCL, Royal Free Hosp, Natl Amyloidosis Ctr, Div Med, London, England Univ Paris Saclay, INSERM, U1195, Dept Neurol, Paris, FranceLow, Soon-Chai论文数: 0 引用数: 0 h-index: 0机构: Univ Malaya, Div Neurol, Dept Med, Kuala Lumpur, Malaysia Univ Paris Saclay, INSERM, U1195, Dept Neurol, Paris, FranceSekijima, Yoshiki论文数: 0 引用数: 0 h-index: 0机构: Shinshu Univ, Sch Med, Dept Med Neurol & Rheumatol, Matsumoto, Nagano, Japan Univ Paris Saclay, INSERM, U1195, Dept Neurol, Paris, FranceObici, Laura论文数: 0 引用数: 0 h-index: 0机构: Fdn IRCCS Policlin San Matteo, Amyloidosis Res & Treatment Ctr, Pavia, Italy Univ Paris Saclay, INSERM, U1195, Dept Neurol, Paris, FranceBlakesley, Rick论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Data Sci & Stat, Cambridge, MA USA Univ Paris Saclay, INSERM, U1195, Dept Neurol, Paris, FranceArum, Seth论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Global Patient Safety & Risk Management, Cambridge, MA USA Univ Paris Saclay, INSERM, U1195, Dept Neurol, Paris, FranceShilling, Rebecca论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Clin Res, Cambridge, MA USA Univ Paris Saclay, INSERM, U1195, Dept Neurol, Paris, FranceVest, John论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Clin Res, Cambridge, MA USA Univ Paris Saclay, INSERM, U1195, Dept Neurol, Paris, FrancePolydefkis, Michael论文数: 0 引用数: 0 h-index: 0机构: Johns Hopkins Univ, Dept Neurol, Baltimore, MD 21218 USA Univ Paris Saclay, INSERM, U1195, Dept Neurol, Paris, France
- [32] Effectiveness of patisiran after switching from tafamidis for the treatment of hereditary transthyretin-mediated amyloidosis with polyneuropathyEUROPEAN JOURNAL OF NEUROLOGY, 2024, 31 (09)Labeyrie, Celine论文数: 0 引用数: 0 h-index: 0机构: Univ Paris Saclay, Assistance Publ Hop Paris AP HP, Ctr Hosp Univ CHU Bicetre, Neurol Dept,CERAMIC,INSERM U1195, 78,Ave Gen Leclerc, F-94270 Le Kremlin Bicetre, France Univ Paris Saclay, Assistance Publ Hop Paris AP HP, Ctr Hosp Univ CHU Bicetre, Neurol Dept,CERAMIC,INSERM U1195, 78,Ave Gen Leclerc, F-94270 Le Kremlin Bicetre, FranceMerkel, Madeline论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA USA Univ Paris Saclay, Assistance Publ Hop Paris AP HP, Ctr Hosp Univ CHU Bicetre, Neurol Dept,CERAMIC,INSERM U1195, 78,Ave Gen Leclerc, F-94270 Le Kremlin Bicetre, FranceSethi, Sakshi论文数: 0 引用数: 0 h-index: 0机构: Anal Grp, Boston, MA USA Univ Paris Saclay, Assistance Publ Hop Paris AP HP, Ctr Hosp Univ CHU Bicetre, Neurol Dept,CERAMIC,INSERM U1195, 78,Ave Gen Leclerc, F-94270 Le Kremlin Bicetre, FrancePopadic, Lyuba论文数: 0 引用数: 0 h-index: 0机构: Anal Grp, Boston, MA USA Univ Paris Saclay, Assistance Publ Hop Paris AP HP, Ctr Hosp Univ CHU Bicetre, Neurol Dept,CERAMIC,INSERM U1195, 78,Ave Gen Leclerc, F-94270 Le Kremlin Bicetre, FranceYang, Hongbo论文数: 0 引用数: 0 h-index: 0机构: Anal Grp, Boston, MA USA Univ Paris Saclay, Assistance Publ Hop Paris AP HP, Ctr Hosp Univ CHU Bicetre, Neurol Dept,CERAMIC,INSERM U1195, 78,Ave Gen Leclerc, F-94270 Le Kremlin Bicetre, FranceSweetser, Marianne T.论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA USA Univ Paris Saclay, Assistance Publ Hop Paris AP HP, Ctr Hosp Univ CHU Bicetre, Neurol Dept,CERAMIC,INSERM U1195, 78,Ave Gen Leclerc, F-94270 Le Kremlin Bicetre, FranceLin, Hollis论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA USA Univ Paris Saclay, Assistance Publ Hop Paris AP HP, Ctr Hosp Univ CHU Bicetre, Neurol Dept,CERAMIC,INSERM U1195, 78,Ave Gen Leclerc, F-94270 Le Kremlin Bicetre, FranceAdams, David论文数: 0 引用数: 0 h-index: 0机构: Univ Paris Saclay, Assistance Publ Hop Paris AP HP, Ctr Hosp Univ CHU Bicetre, Neurol Dept,CERAMIC,INSERM U1195, 78,Ave Gen Leclerc, F-94270 Le Kremlin Bicetre, France Univ Paris Saclay, Assistance Publ Hop Paris AP HP, Ctr Hosp Univ CHU Bicetre, Neurol Dept,CERAMIC,INSERM U1195, 78,Ave Gen Leclerc, F-94270 Le Kremlin Bicetre, France
- [33] LONGTERM TREATMENT EFFECTS OF INOTERSEN ON QUALITY OF LIFE IN PATIENTS WITH HEREDITARY TRANSTHYRETIN-MEDIATED AMYLOIDOSIS WITH POLYNEUROPATHYMUSCLE & NERVE, 2021, 64 : S57 - S57Brown, Duncan论文数: 0 引用数: 0 h-index: 0Karam, Chafic论文数: 0 引用数: 0 h-index: 0Yang, Min论文数: 0 引用数: 0 h-index: 0Done, Nicolae论文数: 0 引用数: 0 h-index: 0Zhu, JingJing论文数: 0 引用数: 0 h-index: 0Greatsinger, Ali论文数: 0 引用数: 0 h-index: 0Bozas, Ana论文数: 0 引用数: 0 h-index: 0Llonch, Montserrat Vera论文数: 0 引用数: 0 h-index: 0Signorovitch, James论文数: 0 引用数: 0 h-index: 0
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- [35] HELIOS-A: 9-month Results from the Phase 3 Study of Vutrisiran in Patients with Hereditary Transthyretin-Mediated Amyloidosis with PolyneuropathyNEUROLOGY, 2021, 96 (15)Adams, David论文数: 0 引用数: 0 h-index: 0机构: Univ Paris Saclay, CHU Bicetre, APHP, Dept Neurol,INSERM U1195, Paris, France Univ Paris Saclay, CHU Bicetre, APHP, Dept Neurol,INSERM U1195, Paris, FranceTournev, Ivailo L.论文数: 0 引用数: 0 h-index: 0机构: Med Univ Sofia, Univ Hosp Aleksandrovska, Dept Neurol, Clin Nervous Dis, Sofia, Bulgaria New Bulgarian Univ, Dept Cognit Sci, Sofia, Bulgaria Univ Paris Saclay, CHU Bicetre, APHP, Dept Neurol,INSERM U1195, Paris, FranceTaylor, Mark S.论文数: 0 引用数: 0 h-index: 0机构: Univ Sydney, Westmead Hosp, Dept Clin Immunol & Allergy, Sydney, NSW, Australia Univ Sydney, Westmead Clin Sch, Sydney, NSW, Australia Univ Paris Saclay, CHU Bicetre, APHP, Dept Neurol,INSERM U1195, Paris, FranceCoelho, Teresa论文数: 0 引用数: 0 h-index: 0机构: Hosp Santo Antonio, Ctr Hosp Porto, Porto, Portugal Univ Paris Saclay, CHU Bicetre, APHP, Dept Neurol,INSERM U1195, Paris, FrancePlante-Bordeneuve, Violaine论文数: 0 引用数: 0 h-index: 0机构: CHU Henri Mondor, Assistance Publ Hop Paris, Neurol Amyloid network, Creteil, France Univ Paris Saclay, CHU Bicetre, APHP, Dept Neurol,INSERM U1195, Paris, FranceBerk, John L.论文数: 0 引用数: 0 h-index: 0机构: Boston Med Ctr, Boston, MA USA Univ Paris Saclay, CHU Bicetre, APHP, Dept Neurol,INSERM U1195, Paris, FranceGonzalez-Duarte, Alejandra论文数: 0 引用数: 0 h-index: 0机构: Inst Nacl Ciencias Medicas Nutr Salvador Zubiran, Madrid, Spain Univ Paris Saclay, CHU Bicetre, APHP, Dept Neurol,INSERM U1195, Paris, FranceGillmore, Julian D.论文数: 0 引用数: 0 h-index: 0机构: UCL, Royal Free Hosp, Natl Amyloidosis Ctr, London, England Univ Paris Saclay, CHU Bicetre, APHP, Dept Neurol,INSERM U1195, Paris, FranceLow, Soon-Chai论文数: 0 引用数: 0 h-index: 0机构: Univ Malaya, Dept Med, Div Neurol, Kuala Lumpur, Malaysia Univ Paris Saclay, CHU Bicetre, APHP, Dept Neurol,INSERM U1195, Paris, FranceSekijima, Yoshiki论文数: 0 引用数: 0 h-index: 0机构: Shinshu Univ, Dept Med Neurol Rheumatol, Sch Med, Matsumoto, Nagano, Japan Univ Paris Saclay, CHU Bicetre, APHP, Dept Neurol,INSERM U1195, Paris, FranceObici, Laura论文数: 0 引用数: 0 h-index: 0机构: IRCCS Fdn Policlin San Matteo, Amyloidosis Res & Treatment Ctr, Pavia, Italy Univ Paris Saclay, CHU Bicetre, APHP, Dept Neurol,INSERM U1195, Paris, FranceBlakesley, Rick论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharm, Cambridge, England Univ Paris Saclay, CHU Bicetre, APHP, Dept Neurol,INSERM U1195, Paris, FranceArum, Seth论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharm, Cambridge, England Univ Paris Saclay, CHU Bicetre, APHP, Dept Neurol,INSERM U1195, Paris, FranceShilling, Rebecca论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharm, Cambridge, England Univ Paris Saclay, CHU Bicetre, APHP, Dept Neurol,INSERM U1195, Paris, FranceVest, John论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharm, Cambridge, England Univ Paris Saclay, CHU Bicetre, APHP, Dept Neurol,INSERM U1195, Paris, FrancePolydefkis, Michael论文数: 0 引用数: 0 h-index: 0机构: Johns Hopkins Univ, Sch Med, Dept Neurol, Baltimore, MD 21218 USA Univ Paris Saclay, CHU Bicetre, APHP, Dept Neurol,INSERM U1195, Paris, France
- [36] Practical Guidance for the Use of Patisiran in the Management of Polyneuropathy in Hereditary Transthyretin-Mediated AmyloidosisTHERAPEUTICS AND CLINICAL RISK MANAGEMENT, 2023, 19 : 973 - 981Dixon, Stacy论文数: 0 引用数: 0 h-index: 0机构: Univ Colorado, Dept Neurol, Aurora, CO USA Univ Colorado, Dept Neurol, Aurora, CO USAKang, Xuan论文数: 0 引用数: 0 h-index: 0机构: Univ Colorado, Dept Neurol, Aurora, CO USA Univ Colorado, Dept Neurol, Aurora, CO USAQuan, Dianna论文数: 0 引用数: 0 h-index: 0机构: Univ Colorado, Dept Neurol, Aurora, CO USA Univ Colorado, Dept Neurol, 12631 East 17th Ave, Mailstop B185, Aurora, CO 80045 USA Univ Colorado, Dept Neurol, Aurora, CO USA
- [37] HELIOS-A: 9-month results from the phase 3 study of vutrisiran in patients with hereditary transthyretin-mediated amyloidosis with polyneuropathyJOURNAL OF THE PERIPHERAL NERVOUS SYSTEM, 2021, 26 (03) : 309 - 309Adams, David论文数: 0 引用数: 0 h-index: 0机构: Univ Paris Saclay, CHU Bicetre, APHP, Neurol Dept,INSERM 1195, Le Kremlin Bicetre, France Univ Paris Saclay, CHU Bicetre, APHP, Neurol Dept,INSERM 1195, Le Kremlin Bicetre, FranceTournev, Ivailo论文数: 0 引用数: 0 h-index: 0机构: Med Univ, Univ Hosp Aleksandrovska, Dept Neurol, Sofia, Bulgaria New Bulgarian Univ, Dept Cognit Sci, Sofia, Bulgaria Univ Paris Saclay, CHU Bicetre, APHP, Neurol Dept,INSERM 1195, Le Kremlin Bicetre, FranceTaylor, Mark论文数: 0 引用数: 0 h-index: 0机构: Univ Sydney, Westmead Hosp, Sydney, NSW, Australia Univ Sydney, Westmead Clin Sch, Sydney, NSW, Australia Univ Paris Saclay, CHU Bicetre, APHP, Neurol Dept,INSERM 1195, Le Kremlin Bicetre, FranceCoelho, Teresa论文数: 0 引用数: 0 h-index: 0机构: Ctr Hosp Porto, Hosp Santo Antonio, Porto, Portugal Univ Paris Saclay, CHU Bicetre, APHP, Neurol Dept,INSERM 1195, Le Kremlin Bicetre, FrancePlante-Bordeneuve, Violaine论文数: 0 引用数: 0 h-index: 0机构: CHU Henri Mondor Assistance Publ Hop Paris, Neurol Amyloid Network, Creteil, France Univ Paris Saclay, CHU Bicetre, APHP, Neurol Dept,INSERM 1195, Le Kremlin Bicetre, FranceBerk, John论文数: 0 引用数: 0 h-index: 0机构: Boston Med Ctr, Boston, MA USA Univ Paris Saclay, CHU Bicetre, APHP, Neurol Dept,INSERM 1195, Le Kremlin Bicetre, FranceGonzalez-Duarte, Alejandra论文数: 0 引用数: 0 h-index: 0机构: Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, Mexico Univ Paris Saclay, CHU Bicetre, APHP, Neurol Dept,INSERM 1195, Le Kremlin Bicetre, FranceGillmore, Julian论文数: 0 引用数: 0 h-index: 0机构: UCL, Royal Free Hosp, Natl Amyloidosis Ctr, London, England Univ Paris Saclay, CHU Bicetre, APHP, Neurol Dept,INSERM 1195, Le Kremlin Bicetre, FranceLow, Soon-Chai论文数: 0 引用数: 0 h-index: 0机构: Univ Malaya, Dept Med, Div Neurol, Kuala Lumpur, Malaysia Univ Paris Saclay, CHU Bicetre, APHP, Neurol Dept,INSERM 1195, Le Kremlin Bicetre, FranceSekijima, Yoshiki论文数: 0 引用数: 0 h-index: 0机构: Shinshu Univ, Sch Med, Dept Med Neurol & Rheumatol, Matsumoto, Nagano, Japan Univ Paris Saclay, CHU Bicetre, APHP, Neurol Dept,INSERM 1195, Le Kremlin Bicetre, FranceObici, Laura论文数: 0 引用数: 0 h-index: 0机构: IRCCS Fdn Policlin San Matteo, Amyloidosis Res & Treatment Ctr, Pavia, Italy Univ Paris Saclay, CHU Bicetre, APHP, Neurol Dept,INSERM 1195, Le Kremlin Bicetre, FranceBlakesley, Rick论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA USA Univ Paris Saclay, CHU Bicetre, APHP, Neurol Dept,INSERM 1195, Le Kremlin Bicetre, FranceArum, Seth论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA USA Univ Paris Saclay, CHU Bicetre, APHP, Neurol Dept,INSERM 1195, Le Kremlin Bicetre, FranceShilling, Rebecca论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA USA Univ Paris Saclay, CHU Bicetre, APHP, Neurol Dept,INSERM 1195, Le Kremlin Bicetre, FranceVest, John论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA USA Univ Paris Saclay, CHU Bicetre, APHP, Neurol Dept,INSERM 1195, Le Kremlin Bicetre, FrancePolydefkis, Michael论文数: 0 引用数: 0 h-index: 0机构: Johns Hopkins Univ, Sch Med, Dept Neurol, Baltimore, MD 21205 USA Univ Paris Saclay, CHU Bicetre, APHP, Neurol Dept,INSERM 1195, Le Kremlin Bicetre, France
- [38] SWITCHING FROM INOTERSEN TO EPLONTERSEN IN PATIENTS WITH HEREDITARY TRANSTHYRETIN AMYLOIDOSIS POLYNEUROPATHYJOURNAL OF THE PERIPHERAL NERVOUS SYSTEM, 2024, 29 : S138 - S139Conceicao, Isabel论文数: 0 引用数: 0 h-index: 0机构: Ctr Hosp Univ Lisboa Norte, Hosp Santa Maria, Lisbon, Portugal Ctr Hosp Univ Lisboa Norte, Hosp Santa Maria, Lisbon, PortugalWeiler, Markus论文数: 0 引用数: 0 h-index: 0机构: Heidelberg Univ Hosp, Amyloidosis Ctr, Heidelberg, Germany Heidelberg Univ Hosp, Dept Neurol, Heidelberg, Germany Ctr Hosp Univ Lisboa Norte, Hosp Santa Maria, Lisbon, PortugalKowacs, Pedro论文数: 0 引用数: 0 h-index: 0机构: Inst Neurol Curitiba, Curitiba, Parana, Brazil Ctr Hosp Univ Lisboa Norte, Hosp Santa Maria, Lisbon, PortugalDasgupta, Noel论文数: 0 引用数: 0 h-index: 0机构: Indiana Univ Sch Med, Indianapolis, IN USA Ctr Hosp Univ Lisboa Norte, Hosp Santa Maria, Lisbon, PortugalKhella, Sami论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Sch Med, Philadelphia, PA USA Ctr Hosp Univ Lisboa Norte, Hosp Santa Maria, Lisbon, PortugalChao, Chi-Chao论文数: 0 引用数: 0 h-index: 0机构: Natl Taiwan Univ Hosp, Taipei, Taiwan Ctr Hosp Univ Lisboa Norte, Hosp Santa Maria, Lisbon, PortugalAttarian, Shahram论文数: 0 引用数: 0 h-index: 0机构: Ctr Hosp Univ La Timone, Neuromuscular Disorders & ALS Dept, Marseille, France Ctr Hosp Univ Lisboa Norte, Hosp Santa Maria, Lisbon, PortugalJung, Shiangtung论文数: 0 引用数: 0 h-index: 0机构: Ionis Pharmaceut Inc, Carlsbad, CA USA Ctr Hosp Univ Lisboa Norte, Hosp Santa Maria, Lisbon, PortugalChen, Jersey论文数: 0 引用数: 0 h-index: 0机构: AstraZeneca, Late Stage Dev Cardiovasc Renal & Metab, BioPharmaceut R&D, Gaithersburg, MD USA Ctr Hosp Univ Lisboa Norte, Hosp Santa Maria, Lisbon, PortugalSchneider, Eugene论文数: 0 引用数: 0 h-index: 0机构: Ionis Pharmaceut Inc, Carlsbad, CA USA Ctr Hosp Univ Lisboa Norte, Hosp Santa Maria, Lisbon, PortugalViney, Nicholas论文数: 0 引用数: 0 h-index: 0机构: Ionis Pharmaceut Inc, Carlsbad, CA USA Ctr Hosp Univ Lisboa Norte, Hosp Santa Maria, Lisbon, PortugalGertz, Morie论文数: 0 引用数: 0 h-index: 0机构: Mayo Clin, Rochester, MN USA Ctr Hosp Univ Lisboa Norte, Hosp Santa Maria, Lisbon, PortugalMasri, Ahmad论文数: 0 引用数: 0 h-index: 0机构: OHSU Ctr Hypertroph Cardiomyopathy & Amyloidosis, Portland, OR USA Ctr Hosp Univ Lisboa Norte, Hosp Santa Maria, Lisbon, PortugalCruz, Marcia Waddington论文数: 0 引用数: 0 h-index: 0机构: Univ Fed Rio de Janeiro, Univ Hosp, Amyloidosis Ctr, CEPARM, Rio De Janeiro, Brazil Ctr Hosp Univ Lisboa Norte, Hosp Santa Maria, Lisbon, PortugalCoelho, Teresa论文数: 0 引用数: 0 h-index: 0机构: Ctr Hosp Univ Santo Antonio, Porto, Portugal Ctr Hosp Univ Lisboa Norte, Hosp Santa Maria, Lisbon, Portugal论文数: 引用数: h-index:机构:
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