Intravitreal enzyme replacement therapy to prevent retinal disease progression in children with neuronal ceroid lipofuscinosis type 2 (CLN2): Unilateral injection results

被引：0
|
作者：
Rogers, David L. [1 ]
de los Reyes, Emily C. [1 ]
Mendel, Thomas A. [2 ]
Caprul, Brian J. [1 ]
Podlasiak, Sarah [1 ]
Jordan, Catherine O. [1 ]
机构：
[1] Nationwide Childrens Hosp, Columbus, OH USA
[2] Ohio State Univ, Wexner Med Ctr, Columbus, OH USA
来源：
MOLECULAR GENETICS AND METABOLISM | 2024年 / 141卷 / 02期
关键词：
D O I：
10.1016/j.ymgme.2023.108019
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
280
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收藏
页数：1
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