Ophthalmologic findings following intrathecal AAV9 mediated gene transfer for Giant Axonal Neuropathy

被引：0
|
作者：
Bharucha-Goebel, D. [1 ,2 ]
Saade, D. [1 ]
Todd, J. [1 ,3 ]
Huryn, L. [4 ]
Norato, G. [3 ]
DeLong, T. [1 ]
Averion, G. [1 ]
Donkervoort, S. [1 ]
Foley, A. [1 ]
Acquaye, N. [1 ]
Mendoza, C. [1 ]
Gray, S. [5 ]
Zein, W. [4 ]
Bonnemann, C. [1 ]
机构：
[1] NIH, Neuromuscular & Neurogenet Disorders Childhood Se, Bethesda, MD USA
[2] Childrens Natl Hosp, Div Neurol, Washington, DC USA
[3] NIH, Off Clin Director, Bethesda, MD USA
[4] NEI, NIH, Bethesda, MD USA
[5] UT Southwestern Med Ctr, Dept Paediat, Dallas, TX USA
来源：
NEUROMUSCULAR DISORDERS | 2023年 / 33卷
关键词：
D O I：
10.1016/j.nmd.2023.07.482
中图分类号：
R74 [神经病学与精神病学];
学科分类号：
摘要：
P444
引用
收藏
页码：S189 / S189
页数：1
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