[1] Childrens Hosp Philadelphia, Div Hematol, Philadelphia, PA 19104 USA
[2] Univ Penn, Dept Pediat, Perelman Sch Med, Philadelphia, PA 19104 USA
[3] Univ Texas Southwestern Med Ctr Dallas, Dept Pediat, Div Hematol & Oncol, Dallas, TX 75390 USA
[4] Univ Iowa Hlth Care, Stead Family Dept Pediat, Carver Coll Med, Iowa City, IA USA
[5] Univ S Florida, Johns Hopkins All Childrens Hosp, Morsani Coll Med, Div Allergy & Immunol,Dept Pediat, St Petersburg, FL USA
[6] Washington Univ, Sch Med, Dept Pediat, St Louis, MO 63110 USA
[7] X4 Pharmaceut Inc, Boston, MA USA
[8] Univ Michigan, CS Mott Childrens Hosp, Ann Arbor, MI 48109 USA