In Vivo Selection in Non-Human Primates Identifies AAV Capsids Having Enhanced Transgene Expression and Biodistribution in Spinal Cord after Intrathecal Administration

被引：0
|
作者：
Maguire, Casey A. [1 ]
Hanlon, Killian S. [1 ]
Kozarsky, Karen [2 ]
Clark, Sean [3 ]
Gong, Yi [4 ]
Cheng, Ming [1 ]
De la Cruz, Demitri [5 ]
Patel, Nikita [1 ]
Santoscoy, Miguel [1 ]
Nguyen, Diane M. [1 ]
Nammour, Josette [1 ]
机构：
[1] Massachusetts Gen Hosp, Charlestown, MA USA
[2] SwanBio Therapeut Ltd, Bala Cynwyd, PA USA
[3] SwanBio Therapeut Ltd, Princeton, NJ USA
[4] Massachusetts Gen Hosp, Boston, MA USA
[5] Massachusetts Gen Hosp, Neurol, Charlestown, MA USA
来源：
MOLECULAR THERAPY | 2023年 / 31卷 / 04期
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
455
引用
收藏
页码：235 / 235
页数：1
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