Development and validation of a novel AAV gene therapy for mucopolysaccharidosis type IIIB in a large animal

被引：0
|
作者：
Banchi, Elena Gaia [1 ]
Alonso, Rafael [1 ]
Jacquot, Sylvie [1 ]
Fransquin, Kevin [1 ]
Courtot, Enora [1 ]
Denis, Timothee De Saint [1 ]
Ausseil, Jerome [2 ]
Piguet, Francoise [1 ]
机构：
[1] Paris Brain Inst, Paris, France
[2] Toulouse Univ Hosp, Toulouse, France
来源：
MOLECULAR GENETICS AND METABOLISM | 2024年 / 141卷 / 02期
关键词：
D O I：
10.1016/j.ymgme.2023.107768
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
29
引用
收藏
页数：1
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