Gene Therapy for Genetic Disease

被引：0
|
作者：
邱信芳
薛京伦
机构：
[1] Fudan University
[2] PRC
[3] Shanghai 200433
[4] State Key Laboratory of Genetic Engineering
来源：
ProgressinNaturalScience | 1994年 / 05期
关键词：
clotting factor IX; gene therapy; gene transfer; hemophilia B;
D O I：
暂无
中图分类号：
R596 [遗传性疾病];
学科分类号：
1002 ; 100201 ;
摘要：
There are more than 4700 kinds of genetic diseases and millions of sufferers worldwide. The deficient genes not only cause suffering to the patients, but bring tragedy to their descendants through heredity.People have been trying to use gene therapy strategy to cure hereditary diseases. With the development of technology, the laboratorial somatic cell gene therapy is moving towards clinical bed and has shown promising prospect. Hemophilia B is one of the several kinds of diseases that are suitable for somatic cell gene therapy owing to its small pathogenic gene and clear genetic
引用
收藏
页码：61 / 69
页数：9
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