COL7A1 repair via prime editing in dystrophic epidermolysis bullosa

被引：0
|
作者：
Bischof, J. [1 ]
Kocher, T. [1 ]
Pedroso, L. Lopes [1 ]
Liemberger, B. [1 ]
Hainzl, S. [1 ]
Maeding, N. [3 ]
Strunk, D. [3 ]
Guttmann-Gruber, C. [1 ]
Wally, V. [1 ]
Hofbauer, J. Pinon [1 ]
Bauer, J. W. [2 ]
Koller, U. [1 ]
机构：
[1] Paracelsus Med Univ, Univ Hosp, Dept Dermatol & Allergol, EB House Austria,Res Program Mol Therapy Genoderm, A-5020 Salzburg, Austria
[2] Paracelsus Med Univ Salzburg, Dept Dermatol & Allergol, Univ Hosp, A-5020 Salzburg, Austria
[3] Paracelsus Med Univ, Cell Therapy Inst, SCI TReCS, Salzburg, Austria
来源：
HUMAN GENE THERAPY | 2024年 / 35卷 / 3-4期
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
P665
引用
收藏
页码：A275 / A276
页数：2
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