COL7A1 repair via prime editing in dystrophic epidermolysis bullosa

被引：0

作者：

Bischof, J. ^{[1
]}

Kocher, T. ^{[1
]}

Pedroso, L. Lopes ^{[1
]}

Liemberger, B. ^{[1
]}

Hainzl, S. ^{[1
]}

Maeding, N. ^{[3
]}

Strunk, D. ^{[3
]}

Guttmann-Gruber, C. ^{[1
]}

Wally, V. ^{[1
]}

Hofbauer, J. Pinon ^{[1
]}

Bauer, J. W. ^{[2
]}

Koller, U. ^{[1
]}

机构：

[1] Paracelsus Med Univ, Univ Hosp, Dept Dermatol & Allergol, EB House Austria,Res Program Mol Therapy Genoderm, A-5020 Salzburg, Austria

[2] Paracelsus Med Univ Salzburg, Dept Dermatol & Allergol, Univ Hosp, A-5020 Salzburg, Austria

[3] Paracelsus Med Univ, Cell Therapy Inst, SCI TReCS, Salzburg, Austria

来源：

HUMAN GENE THERAPY | 2024年 / 35卷 / 3-4期

关键词：

D O I：

暂无

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

P665

引用

页码：A275 / A276

页数：2

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