Targeted genome editing of PMP22 TATA-box reduced PMP22 to therapeutic level in CMT1A patient derived iPSC-Schwann cells

被引：0
|
作者：
Go, N. Y. [1 ]
Lee, K. I. [1 ]
Ahn, C. H. [1 ]
Lee, J. Y. [1 ]
机构：
[1] ToolGen, Seoul, South Korea
来源：
HUMAN GENE THERAPY | 2024年 / 35卷 / 3-4期
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D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
P703
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页码：A289 / A290
页数：2
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