Complete remission after patisiran treatment in a patient with nephrotic syndrome secondary to hereditary transthyretin amyloidosis (ATTR)

被引：0
|
作者：
Vila, Axel [1 ]
Moktefi, Anissa [2 ,3 ]
Damy, Thibaud [4 ,5 ]
Plante-Bordeneuve, Violaine [6 ]
Remy, Philippe [1 ]
Colombat, Magali [7 ]
Audard, Vincent [1 ,2 ]
Sakhi, Hamza [1 ,2 ]
机构：
[1] Hop Univ Henri Mondor, Assistance Publ Hop Paris APHP, Ctr Reference Malad Rare Syndrome Nephrot Idiopath, Serv Nephrol & Transplantat, Creteil, France
[2] Univ Paris Est Creteil, Inst Mondor Rech Biomed IMRB, Inst Natl Sante & Rech Med, INSERM U955, Creteil, France
[3] Hop Univ Henri Mondor, Serv Anatomopathol, Creteil, France
[4] Univ Paris Est Creteil, Equipe CEpiA Clin Epidemiol & Aging, INSERM U955, IMRB, Creteil, France
[5] Hop Univ Henri Mondor, AP HP, Serv Cardiol, GRC Amyloid Res Inst,Ctr Reference Natl Amyloses C, Creteil, France
[6] Hop Univ Henri Mondor, AP HP, GRC Amyloid Res Inst, Serv Neurol, Creteil, France
[7] Ctr Hosp Univ Toulouse, Serv Anatomopathol, Toulouse, France
来源：
AMYLOID-JOURNAL OF PROTEIN FOLDING DISORDERS | 2025年
关键词：
Hereditary Transthyretin Amyloidosis; Nephrotic Syndrome; Patisiran; Tafamidis;
D O I：
10.1080/13506129.2025.2472819
中图分类号：
Q5 [生物化学]; Q7 [分子生物学];
学科分类号：
071010 ; 081704 ;
摘要：
引用
收藏
页数：4
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