Topical In Situ Gene Therapy for the Treatment of Autosomal Recessive Congenital Ichthyosis Patients

被引：0

作者：

Bolsoni, J. ^{[1
]}

Liu, D. ^{[1
]}

Mohabatpour, F. ^{[1
]}

Apaydin, D. C. ^{[4
]}

Sadhnani, G. G. ^{[4
]}

Leung, J. ^{[1
]}

Jan, E. ^{[1
]}

Kulkarni, J. A. ^{[3
]}

Cullis, P. ^{[1
]}

Hedtrich, S. ^{[1
,2
,4
]}

机构：

[1] Univ British Columbia, Vancouver, BC, Canada

[2] Max Delbruck Ctr Mol Med, Berlin, Germany

[3] NanoVat Therapeut, 2405 Wesbrook Mall, Vancouver, BC, Canada

[4] Charite, Berlin, Germany

来源：

HUMAN GENE THERAPY | 2024年 / 35卷 / 3-4期

关键词：

D O I：

暂无

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

P687

引用

页码：A284 / A284

页数：1

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