Preclinical development of an ex vivo gene therapy for Mucopolysaccharidosis type II

被引：0
|
作者：
Poletti, V. [1 ]
Rruga, F. [1 ]
Das, S. [2 ]
Milazzo, R. [3 ]
Dimartino, A. [1 ]
Spadini, S. [1 ]
Politi, L. S. [4 ]
Rizzardi, P. [3 ]
Vallanti, G. [5 ]
Montepeloso, A. [1 ]
Biffi, A.
机构：
[1] Univ Padua, Div Pediat Hematol & Oncol & Stem Cell Transplant, Womans & Child Hlth Dept, Padua, Italy
[2] Harvard Med Sch, Dana Farber Boston Childrens Canc & Blood Disorde, Boston, MA USA
[3] Altheia Sci, Milan, Italy
[4] Humanitas Univ & Hosp, Neuroradiol Dept, Rozzano, Italy
[5] AGC Biol, Milan, Italy
来源：
HUMAN GENE THERAPY | 2024年 / 35卷 / 3-4期
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
P568
引用
收藏
页码：A242 / A243
页数：2
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