A Phase 1 Clinical Trial of High Dose AAV1.SERCA2a in Patients with Heart Failure: Modulation of SERCA2a of Intramyocytic Calcium trafficking in Heart Failure with Reduced Ejection Fraction (MUSIC-HFrEF)

被引:0
|
作者
Jaski, Brian [1 ]
Cheng, Richard [2 ]
Rudy, Jeffrey [3 ]
Li, Ronald A. [4 ]
Hajjar, Roger [3 ]
机构
[1] San Diego Cardiac Ctr, San Diego, CA USA
[2] Univ Calif San Francisco, San Francisco, CA USA
[3] Sardocor Corp, Boston, MA USA
[4] Medera Inc, Boston, MA USA
关键词
D O I
暂无
中图分类号
Q81 [生物工程学(生物技术)]; Q93 [微生物学];
学科分类号
071005 ; 0836 ; 090102 ; 100705 ;
摘要
5
引用
收藏
页码:3 / 3
页数:1
相关论文
共 50 条
  • [31] Acute pleiotropic effects of dapagliflozin in type 2 diabetic patients with heart failure with reduced ejection fraction: a crossover trial
    Ilyas, Fahmida
    Jones, Lynette
    Tee, Su Ling
    Horsfall, Matthew
    Swan, Amy
    Wollaston, Fiona
    Hecker, Tracy
    De Pasquale, Carla
    Thomas, Simeoni
    Chong, William
    Stranks, Steve
    Mangoni, Arduino A.
    Selvanayagam, Joseph B.
    Chew, Derek P.
    De Pasquale, Carmine G.
    ESC HEART FAILURE, 2021, 8 (05): : 4346 - 4352
  • [32] Microvascular Complications of Type 2 Diabetes in Patients With Heart Failure With Mildly Reduced or Preserved Ejection Fraction in the DELIVER Trial
    Presslie, Calum
    Yang, Mingming
    Desai, Akshay S.
    Claggett, Brian
    Vaduganathan, Muthiah
    De Boer, Rudolf A.
    Hernandez, Adrian F.
    Inzucchi, Silvio E.
    Kosiborod, Mikhail N.
    Lam, Carolyn S.
    Martinez, Felipe
    Shah, Sanjiv J.
    Petersson, Magnus
    Langkilde, Anna Maria
    Solomon, Scott D.
    McMurray, John J.
    Jhund, Pardeep S.
    CIRCULATION, 2023, 148
  • [33] Heart failure with recovered ejection fraction: The role of HbA1c level in hospitalized heart failure patients with type 2 diabetes
    Berezin, Alexander E.
    INTERNATIONAL JOURNAL OF CARDIOLOGY, 2023, 370 : 327 - 329
  • [34] Clinical Considerations for Use of SGLT2 Inhibitor Therapy in Patients with Heart Failure and Reduced Ejection Fraction: A Review
    Nisha B. Jhalani
    Advances in Therapy, 2022, 39 : 3472 - 3487
  • [35] Clinical Considerations for Use of SGLT2 Inhibitor Therapy in Patients with Heart Failure and Reduced Ejection Fraction: A Review
    Jhalani, Nisha B.
    ADVANCES IN THERAPY, 2022, 39 (08) : 3472 - 3487
  • [36] CLINICAL CHARACTERISTICS OF PATIENTS AFFECTED BY HEART FAILURE PATIENTS WITH REDUCED EJECTION FRACTION AND UNDERGOING SGLT2I THERAPY
    Alcidi, G.
    Pugliese, R.
    Ioannoni, S.
    Romano, M.
    Granatiero, M.
    Diomede, D.
    Benvenuto, M.
    Correale, M.
    Brunetti, N.
    Gronda, E.
    Iacoviello, M.
    EUROPEAN HEART JOURNAL SUPPLEMENTS, 2023, 25
  • [37] RATIONALE AND DESIGN FOR A PHASE 2 TRIAL OF VERINURAD PLUS ALLOPURINOL IN PATIENTS WITH HEART FAILURE WITH PRESERVED EJECTION FRACTION AND HYPERURICEMIA
    Kitzman, Dalane W.
    Voors, Adriaan
    Mentz, Robert
    Lewis, Gregory
    Perl, Shira
    Myte, Robin
    Bjorck, Karin
    Erlandsson, Fredrik
    Shah, Sanjiv
    JOURNAL OF THE AMERICAN COLLEGE OF CARDIOLOGY, 2021, 77 (18) : 597 - 597
  • [38] HbA1c level is associated with the development of heart failure with recovered ejection fraction in hospitalized heart failure patients with type 2 diabetes
    Yang, Chen Die
    Aihemaiti, Muladili
    Wei, Jin
    Chen, Jia Wei
    Shu, Xin Yi
    Ding, Feng Hua
    Shen, Wei Feng
    Lu, Lin
    Zhang, Rui Yan
    Pan, Wen Qi
    Wang, Xiao Qun
    INTERNATIONAL JOURNAL OF CARDIOLOGY, 2023, 371 : 259 - 265
  • [39] Interleukin-1 blockade in heart failure with preserved ejection fraction: rationale and design of the Diastolic Heart Failure Anakinra Response Trial 2 (D-HART2)
    Van Tassell, Benjamin W.
    Buckley, Leo F.
    Carbone, Salvatore
    Trankle, Cory R.
    Canada, Justin M.
    Dixon, Dave L.
    Abouzaki, Nayef
    Oddi-Erdle, Claudia
    Biondi-Zoccai, Giuseppe
    Arena, Ross
    Abbate, Antonio
    CLINICAL CARDIOLOGY, 2017, 40 (09) : 626 - 632
  • [40] APPLICATION OF THE H2FPEF-SCORE TO A GLOBAL CLINICAL TRIAL OF PATIENTS WITH HEART FAILURE WITH PRESERVED EJECTION FRACTION: THE TOPCAT TRIAL
    Myhre, Peder
    Vaduganathan, Muthiah
    Claggett, Brian
    Lam, Carolyn
    Desai, Akshay
    Anand, Inderjit
    Sweitzer, Nancy K.
    Fang, James
    O'Meara, Eileen
    Shah, Sanjiv
    Shah, Amil
    Lewis, Eldrin
    Rouleau, Jean
    Pitt, Bertram
    Solomon, Scott
    JOURNAL OF THE AMERICAN COLLEGE OF CARDIOLOGY, 2019, 73 (09) : 912 - 912