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- [31] Engineered Capsids for Efficient Gene Delivery to the Retina and CorneaHUMAN GENE THERAPY, 2020, 31 (13-14) : 756 - 774Frederick, Amy论文数: 0 引用数: 0 h-index: 0机构: Sanofi, Rare & Neurol Dis Therapeut Area, Dept Gene Therapy Res, 49 New York Ave, Framingham, MA 01701 USA Sanofi, Rare & Neurol Dis Therapeut Area, Dept Gene Therapy Res, 49 New York Ave, Framingham, MA 01701 USASullivan, Jennifer论文数: 0 引用数: 0 h-index: 0机构: Sanofi, Rare & Neurol Dis Therapeut Area, Dept Gene Therapy Res, 49 New York Ave, Framingham, MA 01701 USA Sanofi, Rare & Neurol Dis Therapeut Area, Dept Gene Therapy Res, 49 New York Ave, Framingham, MA 01701 USALiu, Lin论文数: 0 引用数: 0 h-index: 0机构: Sanofi, Dept BioAnalyt, Framingham, MA 01701 USA Sanofi, Rare & Neurol Dis Therapeut Area, Dept Gene Therapy Res, 49 New York Ave, Framingham, MA 01701 USAAdamowicz, Matthew论文数: 0 引用数: 0 h-index: 0机构: Sanofi, Rare & Neurol Dis Therapeut Area, Dept Gene Therapy Res, 49 New York Ave, Framingham, MA 01701 USA Sanofi, Rare & Neurol Dis Therapeut Area, Dept Gene Therapy Res, 49 New York Ave, Framingham, MA 01701 USALukason, Michael论文数: 0 引用数: 0 h-index: 0机构: Sanofi, Rare & Neurol Dis Therapeut Area, Dept Gene Therapy Res, 49 New York Ave, Framingham, MA 01701 USA Sanofi, Rare & Neurol Dis Therapeut Area, Dept Gene Therapy Res, 49 New York Ave, Framingham, MA 01701 USARaymer, Jasmine论文数: 0 引用数: 0 h-index: 0机构: Sanofi, Rare & Neurol Dis Therapeut Area, Dept Gene Therapy Res, 49 New York Ave, Framingham, MA 01701 USA Sanofi, Rare & Neurol Dis Therapeut Area, Dept Gene Therapy Res, 49 New York Ave, Framingham, MA 01701 USALuo, Zhengyu论文数: 0 引用数: 0 h-index: 0机构: Sanofi, Rare & Neurol Dis Therapeut Area, Dept Gene Therapy Res, 49 New York Ave, Framingham, MA 01701 USA Sanofi, Rare & Neurol Dis Therapeut Area, Dept Gene Therapy Res, 49 New York Ave, Framingham, MA 01701 USAJin, Xiaoying论文数: 0 引用数: 0 h-index: 0机构: Sanofi, Dept BioAnalyt, Framingham, MA 01701 USA Sanofi, Rare & Neurol Dis Therapeut Area, Dept Gene Therapy Res, 49 New York Ave, Framingham, MA 01701 USARao, Kollu Nageswara论文数: 0 引用数: 0 h-index: 0机构: Sanofi, Rare & Neurol Dis Therapeut Area, Dept Gene Therapy Res, 49 New York Ave, Framingham, MA 01701 USA Sanofi, Rare & Neurol Dis Therapeut Area, Dept Gene Therapy Res, 49 New York Ave, Framingham, MA 01701 USAO'Riordan, Catherine论文数: 0 引用数: 0 h-index: 0机构: Sanofi, Rare & Neurol Dis Therapeut Area, Dept Gene Therapy Res, 49 New York Ave, Framingham, MA 01701 USA Sanofi, Rare & Neurol Dis Therapeut Area, Dept Gene Therapy Res, 49 New York Ave, Framingham, MA 01701 USA
- [32] Engineered Capsids for Efficient Gene Delivery to the Retina and CorneaMOLECULAR THERAPY, 2020, 28 (04) : 74 - 75Frederick, Amy论文数: 0 引用数: 0 h-index: 0机构: Sanofi, Gene Therapy Res, Framingham, MA USA Sanofi, Gene Therapy Res, Framingham, MA USASullivan, Jennifer论文数: 0 引用数: 0 h-index: 0机构: Sanofi, Gene Therapy Res, Framingham, MA USA Sanofi, Gene Therapy Res, Framingham, MA USALiu, Lin论文数: 0 引用数: 0 h-index: 0机构: Sanofi, Bioanalyt Dept, Framingham, MA USA Sanofi, Gene Therapy Res, Framingham, MA USAAdamowicz, Matthew论文数: 0 引用数: 0 h-index: 0机构: Sanofi, Gene Therapy Res, Framingham, MA USA Sanofi, Gene Therapy Res, Framingham, MA USALukason, Michael论文数: 0 引用数: 0 h-index: 0机构: Sanofi, Gene Therapy Res, Framingham, MA USA Sanofi, Gene Therapy Res, Framingham, MA USARaymer, Jasmine论文数: 0 引用数: 0 h-index: 0机构: Sanofi, Gene Therapy Res, Framingham, MA USA Sanofi, Gene Therapy Res, Framingham, MA USALuo, Zhengyu论文数: 0 引用数: 0 h-index: 0机构: Sanofi, Gene Therapy Res, Framingham, MA USA Sanofi, Gene Therapy Res, Framingham, MA USAJin, Xiaoying论文数: 0 引用数: 0 h-index: 0机构: Sanofi, Bioanalyt Dept, Framingham, MA USA Sanofi, Gene Therapy Res, Framingham, MA USAKollu, Nageswara论文数: 0 引用数: 0 h-index: 0机构: Sanofi, Gene Therapy Res, Framingham, MA USA Sanofi, Gene Therapy Res, Framingham, MA USAO'Riordan, Catherine论文数: 0 引用数: 0 h-index: 0机构: Sanofi, Gene Therapy Res, Framingham, MA USA Sanofi, Gene Therapy Res, Framingham, MA USA
- [33] Reciprocal mutations of lung-tropic AAV capsids lead to improved transduction propertiesFRONTIERS IN GENOME EDITING, 2023, 5Cooney, Ashley L.论文数: 0 引用数: 0 h-index: 0机构: Univ Iowa, Stead Family Dept Pediat, Iowa City, IA 52242 USA Pappajohn Biomed Inst, Iowa City, IA 52246 USA Univ Iowa, Ctr Cyst Fibrosis Gene Therapy, Iowa City, IA 52242 USA Univ Iowa, Stead Family Dept Pediat, Iowa City, IA 52242 USABrommel, Christian M.论文数: 0 引用数: 0 h-index: 0机构: Univ Iowa, Stead Family Dept Pediat, Iowa City, IA 52242 USA Pappajohn Biomed Inst, Iowa City, IA 52246 USA Univ Iowa, Ctr Cyst Fibrosis Gene Therapy, Iowa City, IA 52242 USA Univ Iowa, Stead Family Dept Pediat, Iowa City, IA 52242 USATraore, Soumba论文数: 0 引用数: 0 h-index: 0机构: Univ Iowa, Stead Family Dept Pediat, Iowa City, IA 52242 USA Pappajohn Biomed Inst, Iowa City, IA 52246 USA Univ Iowa, Ctr Cyst Fibrosis Gene Therapy, Iowa City, IA 52242 USA Univ Iowa, Stead Family Dept Pediat, Iowa City, IA 52242 USANewby, Gregory A.论文数: 0 引用数: 0 h-index: 0机构: Broad Inst Harvard & MIT, Merkin Inst Transformat Technol Healthcare, Cambridge, MA USA Harvard Univ, Dept Chem & Chem Biol, Cambridge, MA USA Harvard Univ, Howard Hughes Med Inst, Cambridge, MA USA Johns Hopkins Univ, Dept Genet Med, Baltimore, MD USA Univ Iowa, Stead Family Dept Pediat, Iowa City, IA 52242 USALiu, David R.论文数: 0 引用数: 0 h-index: 0机构: Broad Inst Harvard & MIT, Merkin Inst Transformat Technol Healthcare, Cambridge, MA USA Harvard Univ, Dept Chem & Chem Biol, Cambridge, MA USA Harvard Univ, Howard Hughes Med Inst, Cambridge, MA USA Univ Iowa, Stead Family Dept Pediat, Iowa City, IA 52242 USAMcCray Jr, Paul B.论文数: 0 引用数: 0 h-index: 0机构: Univ Iowa, Stead Family Dept Pediat, Iowa City, IA 52242 USA Pappajohn Biomed Inst, Iowa City, IA 52246 USA Univ Iowa, Ctr Cyst Fibrosis Gene Therapy, Iowa City, IA 52242 USA Univ Iowa, Stead Family Dept Pediat, Iowa City, IA 52242 USASinn, Patrick L.论文数: 0 引用数: 0 h-index: 0机构: Univ Iowa, Stead Family Dept Pediat, Iowa City, IA 52242 USA Pappajohn Biomed Inst, Iowa City, IA 52246 USA Univ Iowa, Ctr Cyst Fibrosis Gene Therapy, Iowa City, IA 52242 USA Univ Iowa, Stead Family Dept Pediat, Iowa City, IA 52242 USA
- [34] Novel AAV Capsids Display Expansive Transduction and Enhanced Potency in Subretinally Injected MiceMOLECULAR THERAPY, 2019, 27 (04) : 430 - 431Crosson, Sean M.论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Ophthalmol, Gainesville, FL USA Univ Florida, Ophthalmol, Gainesville, FL USAChoudhury, Shreyasi论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Ophthalmol, Gainesville, FL USA Univ Florida, Ophthalmol, Gainesville, FL USAMellen, Russell论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Ophthalmol, Gainesville, FL USA Univ Florida, Ophthalmol, Gainesville, FL USAMakal, Victoria论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Ophthalmol, Gainesville, FL USA Univ Florida, Ophthalmol, Gainesville, FL USAFajardo, Diego论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Ophthalmol, Gainesville, FL USA Univ Florida, Ophthalmol, Gainesville, FL USAPeterson, James J.论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Ophthalmol, Gainesville, FL USA Univ Florida, Ophthalmol, Gainesville, FL USAZhang, Hangning论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Ophthalmol, Gainesville, FL USA Univ Florida, Ophthalmol, Gainesville, FL USADi Pasquale, Giovanni论文数: 0 引用数: 0 h-index: 0机构: Natl Inst Dent & Craniofacial Res, NIH, Bethesda, MD USA Univ Florida, Ophthalmol, Gainesville, FL USAChiorini, Jay A.论文数: 0 引用数: 0 h-index: 0机构: Natl Inst Dent & Craniofacial Res, NIH, Bethesda, MD USA Univ Florida, Ophthalmol, Gainesville, FL USABoye, Sanford L.论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Pediat, Gainesville, FL USA Univ Florida, Powell Gene Therapy Ctr, Gainesville, FL USA Univ Florida, Ophthalmol, Gainesville, FL USABoye, Shannon E.论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Ophthalmol, Gainesville, FL USA Univ Florida, Ophthalmol, Gainesville, FL USA
- [35] Enhancement of AAV Transduction in Muscle Cells In VitroHUMAN GENE THERAPY, 2022, 33 (23-24) : A208 - A209Soustek, M. S.论文数: 0 引用数: 0 h-index: 0机构: Solid Biosci, Cambridge, MA USA Solid Biosci, Cambridge, MA USABurton, C. P.论文数: 0 引用数: 0 h-index: 0机构: Solid Biosci, Cambridge, MA USA Solid Biosci, Cambridge, MA USABoehler, J. F.论文数: 0 引用数: 0 h-index: 0机构: Solid Biosci, Cambridge, MA USA Solid Biosci, Cambridge, MA USAMorris, C.论文数: 0 引用数: 0 h-index: 0机构: Solid Biosci, Cambridge, MA USA Solid Biosci, Cambridge, MA USAMcGonigle, S.论文数: 0 引用数: 0 h-index: 0机构: Solid Biosci, Cambridge, MA USA Solid Biosci, Cambridge, MA USA
- [36] Comparison of CNS Transduction by Different AAV Capsids in Mouse and Non-Human PrimateMOLECULAR THERAPY, 2015, 23 : S37 - S37Goulet, Martin论文数: 0 引用数: 0 h-index: 0机构: Voyager Therapeut, Neurosci, Cambridge, MA USA Voyager Therapeut, Neurosci, Cambridge, MA USAAubin, Justin论文数: 0 引用数: 0 h-index: 0机构: Voyager Therapeut, Neurosci, Cambridge, MA USA Voyager Therapeut, Neurosci, Cambridge, MA USAKells, Adrian P.论文数: 0 引用数: 0 h-index: 0机构: Voyager Therapeut, Neurosci, Cambridge, MA USA Voyager Therapeut, Neurosci, Cambridge, MA USASu, Qin论文数: 0 引用数: 0 h-index: 0机构: UMMS, Gene Therapy Ctr, Worcester, MA USA Voyager Therapeut, Neurosci, Cambridge, MA USAYuan, Shipeng论文数: 0 引用数: 0 h-index: 0机构: Voyager Therapeut, Neurosci, Cambridge, MA USA Voyager Therapeut, Neurosci, Cambridge, MA USARamamoorthi, Kartik论文数: 0 引用数: 0 h-index: 0机构: Voyager Therapeut, Neurosci, Cambridge, MA USA Voyager Therapeut, Neurosci, Cambridge, MA USAKotin, Rob论文数: 0 引用数: 0 h-index: 0机构: Voyager Therapeut, Neurosci, Cambridge, MA USA Voyager Therapeut, Neurosci, Cambridge, MA USAMcLaughlin, James论文数: 0 引用数: 0 h-index: 0机构: Voyager Therapeut, Neurosci, Cambridge, MA USA Voyager Therapeut, Neurosci, Cambridge, MA USAGao, Guangping论文数: 0 引用数: 0 h-index: 0机构: UMMS, Gene Therapy Ctr, Worcester, MA USA Voyager Therapeut, Neurosci, Cambridge, MA USASah, Dinah W. Y.论文数: 0 引用数: 0 h-index: 0机构: Voyager Therapeut, Neurosci, Cambridge, MA USA Voyager Therapeut, Neurosci, Cambridge, MA USA
- [37] Transduction Profiles of Engineered Adeno-Associated Viral Capsids in Mouse and MarmosetMOLECULAR THERAPY, 2020, 28 (04) : 269 - 270Goertsen, David论文数: 0 引用数: 0 h-index: 0机构: CALTECH, Div Biol & Bioengn, Pasadena, CA USA CALTECH, Div Biol & Bioengn, Pasadena, CA USAFlytzanis, Nicholas C.论文数: 0 引用数: 0 h-index: 0机构: CALTECH, Div Biol & Bioengn, Pasadena, CA USA CALTECH, Div Biol & Bioengn, Pasadena, CA USAGoeden, Nick论文数: 0 引用数: 0 h-index: 0机构: CALTECH, Div Biol & Bioengn, Pasadena, CA USA CALTECH, Div Biol & Bioengn, Pasadena, CA USACummins, Alexander论文数: 0 引用数: 0 h-index: 0机构: NIMH, NIH, Bethesda, MD 20892 USA CALTECH, Div Biol & Bioengn, Pasadena, CA USAPickel, James论文数: 0 引用数: 0 h-index: 0机构: NIMH, NIH, Bethesda, MD 20892 USA CALTECH, Div Biol & Bioengn, Pasadena, CA USAGradinaru, Viviana论文数: 0 引用数: 0 h-index: 0机构: CALTECH, Div Biol & Bioengn, Pasadena, CA USA CALTECH, Div Biol & Bioengn, Pasadena, CA USA
- [38] Process and Platform Development for Production and Purification of CNS-Tropic Engineered AAV CapsidsMOLECULAR THERAPY, 2023, 31 (04) : 688 - 689Xie, Zelong论文数: 0 引用数: 0 h-index: 0机构: Sangamo Therapeut Inc, Brisbane, CA USA Sangamo Therapeut Inc, Brisbane, CA USAKim, Taeho论文数: 0 引用数: 0 h-index: 0机构: Sangamo Therapeut Inc, Brisbane, CA USA Sangamo Therapeut Inc, Brisbane, CA USAOjala, David论文数: 0 引用数: 0 h-index: 0机构: Sangamo Therapeut Inc, Richmond, CA USA Sangamo Therapeut Inc, Brisbane, CA USAPadilla, Jada论文数: 0 引用数: 0 h-index: 0机构: Sangamo Therapeut Inc, Brisbane, CA USA Sangamo Therapeut Inc, Brisbane, CA USAYadav, Sandeep论文数: 0 引用数: 0 h-index: 0机构: Sangamo Therapeut Inc, Brisbane, CA USA Sangamo Therapeut Inc, Brisbane, CA USAChikere, Anthony论文数: 0 引用数: 0 h-index: 0机构: Sangamo Therapeut Inc, Brisbane, CA USA Sangamo Therapeut Inc, Brisbane, CA USA
- [39] The Capsid Race: Multiplexed Analysis and Comparison of Rationally Engineered AAV CNS Capsids In VivoMOLECULAR THERAPY, 2023, 31 (04) : 231 - 232Pimentel, Elena论文数: 0 引用数: 0 h-index: 0机构: UniQure Biopharma BV, Amsterdam, Netherlands UniQure Biopharma BV, Amsterdam, NetherlandsKieper, Sebastian论文数: 0 引用数: 0 h-index: 0机构: UniQure BV, Amsterdam, Netherlands UniQure Biopharma BV, Amsterdam, NetherlandsMoreno, Fiona论文数: 0 引用数: 0 h-index: 0机构: UniQure BV, Amsterdam, Netherlands UniQure Biopharma BV, Amsterdam, NetherlandsVan der Zon, Tom论文数: 0 引用数: 0 h-index: 0机构: UniQure Biopharma BV, Amsterdam, Netherlands UniQure Biopharma BV, Amsterdam, NetherlandsBosma, Bas论文数: 0 引用数: 0 h-index: 0机构: UniQure Biopharma BV, Amsterdam, Netherlands UniQure Biopharma BV, Amsterdam, NetherlandsBashir, Noun论文数: 0 引用数: 0 h-index: 0机构: UniQure Biopharma BV, Amsterdam, Netherlands UniQure Biopharma BV, Amsterdam, NetherlandsWaaijer, Stijn论文数: 0 引用数: 0 h-index: 0机构: UniQure Biopharma BV, Amsterdam, Netherlands UniQure Biopharma BV, Amsterdam, NetherlandsEspinosa, Pedro论文数: 0 引用数: 0 h-index: 0机构: UniQure Biopharma BV, Amsterdam, Netherlands UniQure Biopharma BV, Amsterdam, NetherlandsHoogland, Tycho论文数: 0 引用数: 0 h-index: 0机构: UniQure Biopharma BV, Amsterdam, Netherlands UniQure Biopharma BV, Amsterdam, NetherlandsValls, Mercedes论文数: 0 引用数: 0 h-index: 0机构: UniQure Biopharma BV, Amsterdam, Netherlands UniQure Biopharma BV, Amsterdam, NetherlandsPesic, Milja论文数: 0 引用数: 0 h-index: 0机构: UniQure Biopharma BV, Amsterdam, Netherlands UniQure Biopharma BV, Amsterdam, NetherlandsKusuma, Angga论文数: 0 引用数: 0 h-index: 0机构: UniQure b, Amsterdam, Netherlands UniQure Biopharma BV, Amsterdam, Netherlands
- [40] Bioengineered AAV Capsids with Combined High Human Liver Transduction In Vivo and Unique Humoral SeroreactivityMOLECULAR THERAPY, 2018, 26 (01) : 289 - 303Paulk, Nicole K.论文数: 0 引用数: 0 h-index: 0机构: Stanford Univ, Dept Pediat, 269 Campus Dr, Stanford, CA 94305 USA Stanford Univ, Dept Genet, 269 Campus Dr, Stanford, CA 94305 USA Stanford Univ, Dept Pediat, 269 Campus Dr, Stanford, CA 94305 USA论文数: 引用数: h-index:机构:Zhu, Erhua论文数: 0 引用数: 0 h-index: 0机构: Univ Sydney, Childrens Med Res Inst, Translat Vectorol Grp, Sydney, NSW, Australia Stanford Univ, Dept Pediat, 269 Campus Dr, Stanford, CA 94305 USANygaard, Sean论文数: 0 引用数: 0 h-index: 0机构: Oregon Hlth & Sci Univ, Oregon Stem Cell Ctr, Portland, OR 97239 USA Stanford Univ, Dept Pediat, 269 Campus Dr, Stanford, CA 94305 USALi, Bin论文数: 0 引用数: 0 h-index: 0机构: Oregon Hlth & Sci Univ, Oregon Stem Cell Ctr, Portland, OR 97239 USA Stanford Univ, Dept Pediat, 269 Campus Dr, Stanford, CA 94305 USAXu, Jianpeng论文数: 0 引用数: 0 h-index: 0机构: Stanford Univ, Dept Pediat, 269 Campus Dr, Stanford, CA 94305 USA Stanford Univ, Dept Genet, 269 Campus Dr, Stanford, CA 94305 USA Stanford Univ, Dept Pediat, 269 Campus Dr, Stanford, CA 94305 USAChu, Kirk论文数: 0 引用数: 0 h-index: 0机构: Stanford Univ, Dept Pediat, 269 Campus Dr, Stanford, CA 94305 USA Stanford Univ, Dept Genet, 269 Campus Dr, Stanford, CA 94305 USA Stanford Univ, Dept Pediat, 269 Campus Dr, Stanford, CA 94305 USALeborgne, Christian论文数: 0 引用数: 0 h-index: 0机构: Genethon, Evry, France INSERM, U951, Evry, France Stanford Univ, Dept Pediat, 269 Campus Dr, Stanford, CA 94305 USADane, Allison P.论文数: 0 引用数: 0 h-index: 0机构: UCL, Canc Inst, Dept Haematol, London, England Stanford Univ, Dept Pediat, 269 Campus Dr, Stanford, CA 94305 USAHaft, Annelise论文数: 0 引用数: 0 h-index: 0机构: Oregon Hlth & Sci Univ, Oregon Stem Cell Ctr, Portland, OR 97239 USA Stanford Univ, Dept Pediat, 269 Campus Dr, Stanford, CA 94305 USAZhang, Yue论文数: 0 引用数: 0 h-index: 0机构: Stanford Univ, Dept Pediat, 269 Campus Dr, Stanford, CA 94305 USA Stanford Univ, Dept Genet, 269 Campus Dr, Stanford, CA 94305 USA Stanford Univ, Dept Pediat, 269 Campus Dr, Stanford, CA 94305 USAZhang, Feijie论文数: 0 引用数: 0 h-index: 0机构: Stanford Univ, Dept Pediat, 269 Campus Dr, Stanford, CA 94305 USA Stanford Univ, Dept Genet, 269 Campus Dr, Stanford, CA 94305 USA Stanford Univ, Dept Pediat, 269 Campus Dr, Stanford, CA 94305 USAMorton, Chris论文数: 0 引用数: 0 h-index: 0机构: St Jude Childrens Res Hosp, Dept Surg, Memphis, TN 38105 USA Stanford Univ, Dept Pediat, 269 Campus Dr, Stanford, CA 94305 USAValentine, Marcus B.论文数: 0 引用数: 0 h-index: 0机构: St Jude Childrens Res Hosp, Cytogenet Shared Resource, Memphis, TN 38105 USA Stanford Univ, Dept Pediat, 269 Campus Dr, Stanford, CA 94305 USADavidoff, Andrew M.论文数: 0 引用数: 0 h-index: 0机构: St Jude Childrens Res Hosp, Dept Surg, Memphis, TN 38105 USA Stanford Univ, Dept Pediat, 269 Campus Dr, Stanford, CA 94305 USANathwani, Amit C.论文数: 0 引用数: 0 h-index: 0机构: UCL, Canc Inst, Dept Haematol, London, England Royal Free London NHS Fdn Trust Hosp, Dept Haematol, London, England Royal Free London NHS Fdn Trust Hosp, Katharine Dormandy Haemophilia Ctr, London, England Royal Free London NHS Fdn Trust Hosp, Thrombosis Unit, London, England Natl Hlth Serv Blood & Transplant, Watford, England Stanford Univ, Dept Pediat, 269 Campus Dr, Stanford, CA 94305 USAMingozzi, Federico论文数: 0 引用数: 0 h-index: 0机构: Genethon, Evry, France INSERM, U951, Evry, France Univ Paris 06, Paris, France Stanford Univ, Dept Pediat, 269 Campus Dr, Stanford, CA 94305 USA论文数: 引用数: h-index:机构:Alexander, Ian E.论文数: 0 引用数: 0 h-index: 0机构: Stanford Univ, Dept Pediat, 269 Campus Dr, Stanford, CA 94305 USALisowski, Leszek论文数: 0 引用数: 0 h-index: 0机构: Univ Sydney, Childrens Med Res Inst, Translat Vectorol Grp, Sydney, NSW, Australia MIHE, Pulawy, Poland Stanford Univ, Dept Pediat, 269 Campus Dr, Stanford, CA 94305 USAKay, Mark A.论文数: 0 引用数: 0 h-index: 0机构: Stanford Univ, Dept Pediat, 269 Campus Dr, Stanford, CA 94305 USA Stanford Univ, Dept Genet, 269 Campus Dr, Stanford, CA 94305 USA Stanford Univ, Dept Pediat, 269 Campus Dr, Stanford, CA 94305 USA