Peripheral and Behavioral Impacts of AAV Gene Therapy in a Mouse Model of Niemann-Pick Disease, Type C1

被引：0
|
作者：
Epstein, Benjamin E. [1 ]
Soden, Gabrielle M. [1 ]
Incao, Arturo A. [1 ]
Pavan, William J. [1 ]
机构：
[1] NHGRI, NIH, Bethesda, MD USA
来源：
MOLECULAR THERAPY | 2024年 / 32卷 / 04期
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D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
1574
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页码：734 / 735
页数：2
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