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- [43] Base Editing Eliminates the Sickle Cell Mutation and Pathology in Hematopoietic Stem Cells Derived Erythroid CellsBLOOD, 2020, 136Yen, Jonathan S.论文数: 0 引用数: 0 h-index: 0Newby, Gregory A.论文数: 0 引用数: 0 h-index: 0Mayuranathan, Thiyagaraj论文数: 0 引用数: 0 h-index: 0Porter, Shaina N.论文数: 0 引用数: 0 h-index: 0Yao, Yu论文数: 0 引用数: 0 h-index: 0Woodard, Kaitly J.论文数: 0 引用数: 0 h-index: 0Mayberry, Kalin论文数: 0 引用数: 0 h-index: 0Everette, Kelcee论文数: 0 引用数: 0 h-index: 0Zhang, Jingjing论文数: 0 引用数: 0 h-index: 0Henderson, Jordana M.论文数: 0 引用数: 0 h-index: 0Mccaffrey, Anton P.论文数: 0 引用数: 0 h-index: 0Yen, Jonathan论文数: 0 引用数: 0 h-index: 0Tisdale, John F.论文数: 0 引用数: 0 h-index: 0Tsai, Shengdar Q.论文数: 0 引用数: 0 h-index: 0Liu, David R.论文数: 0 引用数: 0 h-index: 0Weiss, Mitchell J.论文数: 0 引用数: 0 h-index: 0
- [44] Genotoxic Effects of Culture Media on Human Pluripotent Stem CellsSCIENTIFIC REPORTS, 2017, 7Bangalore, Megha Prakash论文数: 0 引用数: 0 h-index: 0机构: Natl Ctr Biol Sci TIFR, Bangalore 560065, Karnataka, India Manipal Univ, Manipal 576104, Karnataka, India Natl Ctr Biol Sci TIFR, Bangalore 560065, Karnataka, IndiaAdhikarla, Syama论文数: 0 引用数: 0 h-index: 0机构: Inst Stem Cell Biol & Regenerat Med, Bangalore 560065, Karnataka, India Natl Ctr Biol Sci TIFR, Bangalore 560065, Karnataka, IndiaMukherjee, Odity论文数: 0 引用数: 0 h-index: 0机构: Inst Stem Cell Biol & Regenerat Med, Bangalore 560065, Karnataka, India Natl Ctr Biol Sci TIFR, Bangalore 560065, Karnataka, IndiaPanicker, Mitradas M.论文数: 0 引用数: 0 h-index: 0机构: Natl Ctr Biol Sci TIFR, Bangalore 560065, Karnataka, India Natl Ctr Biol Sci TIFR, Bangalore 560065, Karnataka, India
- [45] Genotoxic Effects of Culture Media on Human Pluripotent Stem CellsScientific Reports, 7Megha Prakash Bangalore论文数: 0 引用数: 0 h-index: 0机构: National Centre for Biological Sciences (TIFR),Syama Adhikarla论文数: 0 引用数: 0 h-index: 0机构: National Centre for Biological Sciences (TIFR),Odity Mukherjee论文数: 0 引用数: 0 h-index: 0机构: National Centre for Biological Sciences (TIFR),Mitradas M. Panicker论文数: 0 引用数: 0 h-index: 0机构: National Centre for Biological Sciences (TIFR),
- [46] Efficient and in situ correction of hemoglobin Constant Spring mutation by prime editing in human hematopoietic cellsMOLECULAR THERAPY NUCLEIC ACIDS, 2024, 35 (04):Shao, Congwen论文数: 0 引用数: 0 h-index: 0机构: Southern Med Univ, Nanfang Hosp, Innovat Ctr Diagnost & Treatment Thalassemia, Guangzhou 510515, Guangdong, Peoples R China Southern Med Univ, Guangdong Engn & Technol Res Ctr Mol Diagnost Huma, Sch Basic Med Sci, Dept Med Genet, Guangzhou 510515, Guangdong, Peoples R China Southern Med Univ, Nanfang Hosp, Innovat Ctr Diagnost & Treatment Thalassemia, Guangzhou 510515, Guangdong, Peoples R ChinaLiu, Qing论文数: 0 引用数: 0 h-index: 0机构: Southern Med Univ, Nanfang Hosp, Innovat Ctr Diagnost & Treatment Thalassemia, Guangzhou 510515, Guangdong, Peoples R China Southern Med Univ, Guangdong Engn & Technol Res Ctr Mol Diagnost Huma, Sch Basic Med Sci, Dept Med Genet, Guangzhou 510515, Guangdong, Peoples R China Southern Med Univ, Nanfang Hosp, Innovat Ctr Diagnost & Treatment Thalassemia, Guangzhou 510515, Guangdong, Peoples R ChinaXu, Jinchao论文数: 0 引用数: 0 h-index: 0机构: Soochow Univ, Cyrus Tang Med Inst, Natl Clin Res Ctr Hematol Dis, Collaborat Innovat Ctr Hematol,State Key Lab Radia, Suzhou 215123, Jiangsu, Peoples R China Southern Med Univ, Nanfang Hosp, Innovat Ctr Diagnost & Treatment Thalassemia, Guangzhou 510515, Guangdong, Peoples R ChinaZhang, Jianxiang论文数: 0 引用数: 0 h-index: 0机构: Soochow Univ, Cyrus Tang Med Inst, Natl Clin Res Ctr Hematol Dis, Collaborat Innovat Ctr Hematol,State Key Lab Radia, Suzhou 215123, Jiangsu, Peoples R China Southern Med Univ, Nanfang Hosp, Innovat Ctr Diagnost & Treatment Thalassemia, Guangzhou 510515, Guangdong, Peoples R ChinaZhang, Chengpeng论文数: 0 引用数: 0 h-index: 0机构: Soochow Univ, Cyrus Tang Med Inst, Natl Clin Res Ctr Hematol Dis, Collaborat Innovat Ctr Hematol,State Key Lab Radia, Suzhou 215123, Jiangsu, Peoples R China Southern Med Univ, Nanfang Hosp, Innovat Ctr Diagnost & Treatment Thalassemia, Guangzhou 510515, Guangdong, Peoples R ChinaXin, Ye论文数: 0 引用数: 0 h-index: 0机构: Soochow Univ, Cyrus Tang Med Inst, Natl Clin Res Ctr Hematol Dis, Collaborat Innovat Ctr Hematol,State Key Lab Radia, Suzhou 215123, Jiangsu, Peoples R China Southern Med Univ, Nanfang Hosp, Innovat Ctr Diagnost & Treatment Thalassemia, Guangzhou 510515, Guangdong, Peoples R ChinaYe, Yuhua论文数: 0 引用数: 0 h-index: 0机构: Southern Med Univ, Nanfang Hosp, Innovat Ctr Diagnost & Treatment Thalassemia, Guangzhou 510515, Guangdong, Peoples R China Southern Med Univ, Guangdong Engn & Technol Res Ctr Mol Diagnost Huma, Sch Basic Med Sci, Dept Med Genet, Guangzhou 510515, Guangdong, Peoples R China Southern Med Univ, Nanfang Hosp, Innovat Ctr Diagnost & Treatment Thalassemia, Guangzhou 510515, Guangdong, Peoples R ChinaLin, Bin论文数: 0 引用数: 0 h-index: 0机构: Guangzhou Jiexu Gene Technol Co Ltd, Guangzhou 510535, Guangdong, Peoples R China Southern Med Univ, Nanfang Hosp, Innovat Ctr Diagnost & Treatment Thalassemia, Guangzhou 510515, Guangdong, Peoples R ChinaZhang, Xinhua论文数: 0 引用数: 0 h-index: 0机构: 923rd Hosp Peoples Liberat Army, Dept Hematol, Nanning 530021, Guangxi, Peoples R China Southern Med Univ, Nanfang Hosp, Innovat Ctr Diagnost & Treatment Thalassemia, Guangzhou 510515, Guangdong, Peoples R ChinaCheng, Li论文数: 0 引用数: 0 h-index: 0机构: Soochow Univ, Cyrus Tang Med Inst, Natl Clin Res Ctr Hematol Dis, Collaborat Innovat Ctr Hematol,State Key Lab Radia, Suzhou 215123, Jiangsu, Peoples R China Southern Med Univ, Nanfang Hosp, Innovat Ctr Diagnost & Treatment Thalassemia, Guangzhou 510515, Guangdong, Peoples R ChinaXu, Xiangmin论文数: 0 引用数: 0 h-index: 0机构: Southern Med Univ, Nanfang Hosp, Innovat Ctr Diagnost & Treatment Thalassemia, Guangzhou 510515, Guangdong, Peoples R China Southern Med Univ, Guangdong Engn & Technol Res Ctr Mol Diagnost Huma, Sch Basic Med Sci, Dept Med Genet, Guangzhou 510515, Guangdong, Peoples R China Southern Med Univ, Nanfang Hosp, Innovat Ctr Diagnost & Treatment Thalassemia, Guangzhou 510515, Guangdong, Peoples R ChinaXu, Peng论文数: 0 引用数: 0 h-index: 0机构: Soochow Univ, Cyrus Tang Med Inst, Natl Clin Res Ctr Hematol Dis, Collaborat Innovat Ctr Hematol,State Key Lab Radia, Suzhou 215123, Jiangsu, Peoples R China Southern Med Univ, Nanfang Hosp, Innovat Ctr Diagnost & Treatment Thalassemia, Guangzhou 510515, Guangdong, Peoples R China
- [47] Genetic editing of HLA expression in hematopoietic stem cells to broaden their human applicationScientific Reports, 6Hiroki Torikai论文数: 0 引用数: 0 h-index: 0机构: The University of Texas MD Anderson Cancer Center,Division of PediatricsTiejuan Mi论文数: 0 引用数: 0 h-index: 0机构: The University of Texas MD Anderson Cancer Center,Division of PediatricsLoren Gragert论文数: 0 引用数: 0 h-index: 0机构: The University of Texas MD Anderson Cancer Center,Division of PediatricsMartin Maiers论文数: 0 引用数: 0 h-index: 0机构: The University of Texas MD Anderson Cancer Center,Division of PediatricsAmer Najjar论文数: 0 引用数: 0 h-index: 0机构: The University of Texas MD Anderson Cancer Center,Division of PediatricsSonny Ang论文数: 0 引用数: 0 h-index: 0机构: The University of Texas MD Anderson Cancer Center,Division of PediatricsSourindra Maiti论文数: 0 引用数: 0 h-index: 0机构: The University of Texas MD Anderson Cancer Center,Division of PediatricsJianliang Dai论文数: 0 引用数: 0 h-index: 0机构: The University of Texas MD Anderson Cancer Center,Division of PediatricsKirsten C. Switzer论文数: 0 引用数: 0 h-index: 0机构: The University of Texas MD Anderson Cancer Center,Division of PediatricsHelen Huls论文数: 0 引用数: 0 h-index: 0机构: The University of Texas MD Anderson Cancer Center,Division of PediatricsGladys P. Dulay论文数: 0 引用数: 0 h-index: 0机构: The University of Texas MD Anderson Cancer Center,Division of PediatricsAndreas Reik论文数: 0 引用数: 0 h-index: 0机构: The University of Texas MD Anderson Cancer Center,Division of PediatricsEdward J. Rebar论文数: 0 引用数: 0 h-index: 0机构: The University of Texas MD Anderson Cancer Center,Division of PediatricsMichael C. Holmes论文数: 0 引用数: 0 h-index: 0机构: The University of Texas MD Anderson Cancer Center,Division of PediatricsPhilip D. Gregory论文数: 0 引用数: 0 h-index: 0机构: The University of Texas MD Anderson Cancer Center,Division of PediatricsRichard E. Champlin论文数: 0 引用数: 0 h-index: 0机构: The University of Texas MD Anderson Cancer Center,Division of PediatricsElizabeth J. Shpall论文数: 0 引用数: 0 h-index: 0机构: The University of Texas MD Anderson Cancer Center,Division of PediatricsLaurence J. N. Cooper论文数: 0 引用数: 0 h-index: 0机构: The University of Texas MD Anderson Cancer Center,Division of Pediatrics
- [48] Genetic editing of HLA expression in hematopoietic stem cells to broaden their human applicationSCIENTIFIC REPORTS, 2016, 6Torikai, Hiroki论文数: 0 引用数: 0 h-index: 0机构: Univ Texas MD Anderson Canc Ctr, Div Pediat, Houston, TX 77030 USA Univ Texas MD Anderson Canc Ctr, Div Pediat, Houston, TX 77030 USAMi, Tiejuan论文数: 0 引用数: 0 h-index: 0机构: Univ Texas MD Anderson Canc Ctr, Div Pediat, Houston, TX 77030 USA Univ Texas MD Anderson Canc Ctr, Div Pediat, Houston, TX 77030 USAGragert, Loren论文数: 0 引用数: 0 h-index: 0机构: Natl Marrow Donor Program, Bioinformat Res, Minneapolis, MN USA Univ Texas MD Anderson Canc Ctr, Div Pediat, Houston, TX 77030 USAMaiers, Martin论文数: 0 引用数: 0 h-index: 0机构: Natl Marrow Donor Program, Bioinformat Res, Minneapolis, MN USA Univ Texas MD Anderson Canc Ctr, Div Pediat, Houston, TX 77030 USANajjar, Amer论文数: 0 引用数: 0 h-index: 0机构: Univ Texas MD Anderson Canc Ctr, Div Pediat, Houston, TX 77030 USA Univ Texas MD Anderson Canc Ctr, Div Pediat, Houston, TX 77030 USAAng, Sonny论文数: 0 引用数: 0 h-index: 0机构: Univ Texas MD Anderson Canc Ctr, Div Pediat, Houston, TX 77030 USA Univ Texas MD Anderson Canc Ctr, Div Pediat, Houston, TX 77030 USAMaiti, Sourindra论文数: 0 引用数: 0 h-index: 0机构: Univ Texas MD Anderson Canc Ctr, Div Pediat, Houston, TX 77030 USA Univ Texas MD Anderson Canc Ctr, Div Pediat, Houston, TX 77030 USADai, Jianliang论文数: 0 引用数: 0 h-index: 0机构: Univ Texas MD Anderson Canc Ctr, Dept Biostat, Houston, TX 77030 USA Univ Texas MD Anderson Canc Ctr, Div Pediat, Houston, TX 77030 USASwitzer, Kirsten C.论文数: 0 引用数: 0 h-index: 0机构: Univ Texas MD Anderson Canc Ctr, Div Pediat, Houston, TX 77030 USA Univ Texas MD Anderson Canc Ctr, Div Pediat, Houston, TX 77030 USAHuls, Helen论文数: 0 引用数: 0 h-index: 0机构: Univ Texas MD Anderson Canc Ctr, Div Pediat, Houston, TX 77030 USA Univ Texas MD Anderson Canc Ctr, Div Pediat, Houston, TX 77030 USADulay, Gladys P.论文数: 0 引用数: 0 h-index: 0机构: Sangamo BioSci Inc, Richmond, CA USA Univ Texas MD Anderson Canc Ctr, Div Pediat, Houston, TX 77030 USAReik, Andreas论文数: 0 引用数: 0 h-index: 0机构: Sangamo BioSci Inc, Richmond, CA USA Univ Texas MD Anderson Canc Ctr, Div Pediat, Houston, TX 77030 USARebar, Edward J.论文数: 0 引用数: 0 h-index: 0机构: Sangamo BioSci Inc, Richmond, CA USA Univ Texas MD Anderson Canc Ctr, Div Pediat, Houston, TX 77030 USAHolmes, Michael C.论文数: 0 引用数: 0 h-index: 0机构: Sangamo BioSci Inc, Richmond, CA USA Univ Texas MD Anderson Canc Ctr, Div Pediat, Houston, TX 77030 USAGregory, Philip D.论文数: 0 引用数: 0 h-index: 0机构: Sangamo BioSci Inc, Richmond, CA USA Univ Texas MD Anderson Canc Ctr, Div Pediat, Houston, TX 77030 USAChamplin, Richard E.论文数: 0 引用数: 0 h-index: 0机构: Univ Texas MD Anderson Canc Ctr, Div Canc Med, Dept Stem Cell Transplantat & Cellular Therapy, Houston, TX 77030 USA Univ Texas MD Anderson Canc Ctr, Div Pediat, Houston, TX 77030 USAShpall, Elizabeth J.论文数: 0 引用数: 0 h-index: 0机构: Univ Texas MD Anderson Canc Ctr, Div Canc Med, Dept Stem Cell Transplantat & Cellular Therapy, Houston, TX 77030 USA Univ Texas MD Anderson Canc Ctr, Div Pediat, Houston, TX 77030 USACooper, Laurence J. N.论文数: 0 引用数: 0 h-index: 0机构: Univ Texas MD Anderson Canc Ctr, Div Pediat, Houston, TX 77030 USA Ziopharm Oncol Inc, Boston, MA USA Univ Texas MD Anderson Canc Ctr, Div Pediat, Houston, TX 77030 USA
- [49] CRISPR/Cas9 genome editing in human hematopoietic stem cellsNature Protocols, 2018, 13 : 358 - 376Rasmus O Bak论文数: 0 引用数: 0 h-index: 0机构: Stanford University,Department of PediatricsDaniel P Dever论文数: 0 引用数: 0 h-index: 0机构: Stanford University,Department of PediatricsMatthew H Porteus论文数: 0 引用数: 0 h-index: 0机构: Stanford University,Department of Pediatrics
- [50] CRISPR/Cas9 genome editing in human hematopoietic stem cellsNATURE PROTOCOLS, 2018, 13 (02) : 358 - 376Bak, Rasmus O.论文数: 0 引用数: 0 h-index: 0机构: Stanford Univ, Dept Pediat, Stanford, CA 94305 USA Stanford Univ, Dept Pediat, Stanford, CA 94305 USADever, Daniel P.论文数: 0 引用数: 0 h-index: 0机构: Stanford Univ, Dept Pediat, Stanford, CA 94305 USA Stanford Univ, Dept Pediat, Stanford, CA 94305 USAPorteus, Matthew H.论文数: 0 引用数: 0 h-index: 0机构: Stanford Univ, Dept Pediat, Stanford, CA 94305 USA Stanford Univ, Dept Pediat, Stanford, CA 94305 USA