A comparison of different strategies for CRISPR/Cas9-based gene therapies of congenital neutropenia associated with ELANE mutations

被引：0
|
作者：
Ritter, M. U. [1 ,2 ]
Nasri, M. [1 ,2 ]
Dannenmann, B. [1 ,2 ]
Mir, P. [2 ]
Secker, B. [2 ]
Zeidler, C. [3 ,4 ]
Klimiankou, M. [1 ,2 ,3 ,4 ]
Welte, K. [2 ,3 ,4 ]
Skokowa, J. [1 ,2 ,3 ,4 ]
机构：
[1] GRTC Tubingen, Tubingen, Germany
[2] Univ Hosp Tubingen, Tubingen, Germany
[3] Severe Congenital Neutropenia Int Registry Europe, Tubingen, Germany
[4] EuNet INNOCHRON, Iraklion, Greece
来源：
HUMAN GENE THERAPY | 2024年 / 35卷 / 3-4期
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
P385
引用
收藏
页码：A175 / A175
页数：1
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