Risdiplam for Prenatal Therapy of Spinal Muscular Atrophy

被引：0
|
作者：
Finkel, Richard S. [1 ]
Hughes, Samuel H. [1 ]
Parker, Julieann [2 ]
Civitello, Matthew [1 ]
Lavado, Alfonso [1 ]
Mefford, Heather C. [1 ]
Mueller, Lutz [3 ]
Kletzl, Heidemarie [3 ]
Prenatal SMA Risdiplam Study Grp
机构：
[1] St Jude Childrens Res Hosp, Memphis, TN 38105 USA
[2] ObGyn Partners Augusta, Augusta, GA USA
[3] F Hoffmann La Roche, Basel, Switzerland
来源：
NEW ENGLAND JOURNAL OF MEDICINE | 2025年
关键词：
D O I：
10.1056/NEJMc2300802
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
引用
收藏
页数：3
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