In Vivo Lentiviral Gene Therapy for Arc Syndrome

被引：0

作者：

Cozmescu, Andrei Claudiu ^{[1
,2
]}

Touramanidou, Loukia ^{[1
]}

Gurung, Sonam ^{[1
]}

Perocheau, Dany ^{[1
]}

Hu, Yi-Ting ^{[1
]}

Counsell, John R. ^{[3
]}

Karda, Rajvinder ^{[4
]}

Waddington, Simon ^{[4
]}

Baruteau, Julien ^{[1
,2
,5
]}

Turchiano, Giandomenico ^{[1
]}

Gissen, Paul ^{[1
,2
,5
]}

机构：

[1] UCL, Great Ormond St Inst Child Hlth, London, England

[2] NIHR Great Ormond St Hosp, Biomed Res Ctr, London, England

[3] UCL, Div Surg & Intervent Sci, Res Dept Targeted Intervent, London, England

[4] UCL, EGA Inst Womens Hlth, London, England

[5] Great Ormond St Hosp Children NHS Fdn Trust, Metab Med, London, England

来源：

MOLECULAR THERAPY | 2024年 / 32卷 / 04期

关键词：

D O I：

暂无

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

209

引用

页码：112 / 112

页数：1

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