Gene Therapy Approach for Neurofibromatosis Type 1 via Cell-Specific Epigenetic Editing in Schwann Cells

被引：0

作者：

Guglielmi, Adele ^{[1
]}

Miller, Max ^{[1
]}

Punjya, Niraj R. ^{[1
]}

Beitnere, Ulrika ^{[2
]}

Salter-Cid, Tomas ^{[1
]}

Caputo, Claire ^{[1
]}

Sims, Kenneth ^{[3
]}

Fink, Kyle D. ^{[4
]}

O'Geen, Henriette ^{[1
]}

Segal, David J. ^{[1
]}

机构：

[1] Univ Calif Davis, Genome Ctr, Davis, CA USA

[2] Max Delbruck Ctr Mol Med, Mol Biol, Berlin, Germany

[3] Battelle Mem Inst, Battelles Adv Mat & Energet Grp, Columbus, OH USA

[4] Univ Calif Davis, Inst Regenerat Cures, Sacramento, CA USA

来源：

MOLECULAR THERAPY | 2024年 / 32卷 / 04期

关键词：

D O I：

暂无

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

1667.

引用

页码：779 / 779

页数：1

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