共 50 条
- [1] A novel AAV Vector for gene therapy of RPE-related retinal degenerative diseases via intravitreal deliveryMOLECULAR NEURODEGENERATION, 2024, 19 (01)Gong, Yajun论文数: 0 引用数: 0 h-index: 0机构: Sun Yat Sen Univ, Zhongshan Ophthalm Ctr, State Key Lab Ophthalmol, 54 Xianlie South Rd, Guangzhou 510060, Peoples R China Sun Yat Sen Univ, Guangdong Prov Key Lab Ophthalmol & Visual Sci, Guangzhou 510060, Peoples R China Sun Yat Sen Univ, Zhongshan Ophthalm Ctr, State Key Lab Ophthalmol, 54 Xianlie South Rd, Guangzhou 510060, Peoples R ChinaHuang, Xianyu论文数: 0 引用数: 0 h-index: 0机构: Shanghai EmayGene Biotech Co Ltd, Shanghai 201203, Peoples R China Sun Yat Sen Univ, Zhongshan Ophthalm Ctr, State Key Lab Ophthalmol, 54 Xianlie South Rd, Guangzhou 510060, Peoples R ChinaTu, Tianxiang论文数: 0 引用数: 0 h-index: 0机构: Sun Yat Sen Univ, Zhongshan Ophthalm Ctr, State Key Lab Ophthalmol, 54 Xianlie South Rd, Guangzhou 510060, Peoples R China Sun Yat Sen Univ, Guangdong Prov Key Lab Ophthalmol & Visual Sci, Guangzhou 510060, Peoples R China Sun Yat Sen Univ, Zhongshan Ophthalm Ctr, State Key Lab Ophthalmol, 54 Xianlie South Rd, Guangzhou 510060, Peoples R ChinaChu, Cenfeng论文数: 0 引用数: 0 h-index: 0机构: ShanghaiTech Univ, iHuman Inst, Shanghai 201210, Peoples R China ShanghaiTech Univ, Sch Life Sci & Technol, Shanghai 201210, Peoples R China Sun Yat Sen Univ, Zhongshan Ophthalm Ctr, State Key Lab Ophthalmol, 54 Xianlie South Rd, Guangzhou 510060, Peoples R ChinaXian, Chunrui论文数: 0 引用数: 0 h-index: 0机构: ShanghaiTech Univ, iHuman Inst, Shanghai 201210, Peoples R China ShanghaiTech Univ, Sch Life Sci & Technol, Shanghai 201210, Peoples R China Sun Yat Sen Univ, Zhongshan Ophthalm Ctr, State Key Lab Ophthalmol, 54 Xianlie South Rd, Guangzhou 510060, Peoples R ChinaYuan, Yushun论文数: 0 引用数: 0 h-index: 0机构: Shanghai EmayGene Biotech Co Ltd, Shanghai 201203, Peoples R China Sun Yat Sen Univ, Zhongshan Ophthalm Ctr, State Key Lab Ophthalmol, 54 Xianlie South Rd, Guangzhou 510060, Peoples R ChinaFu, Xin论文数: 0 引用数: 0 h-index: 0机构: Sun Yat Sen Univ, Zhongshan Ophthalm Ctr, State Key Lab Ophthalmol, 54 Xianlie South Rd, Guangzhou 510060, Peoples R China Sun Yat Sen Univ, Guangdong Prov Key Lab Ophthalmol & Visual Sci, Guangzhou 510060, Peoples R China Sun Yat Sen Univ, Zhongshan Ophthalm Ctr, State Key Lab Ophthalmol, 54 Xianlie South Rd, Guangzhou 510060, Peoples R ChinaLi, Ruobi论文数: 0 引用数: 0 h-index: 0机构: Sun Yat Sen Univ, Zhongshan Ophthalm Ctr, State Key Lab Ophthalmol, 54 Xianlie South Rd, Guangzhou 510060, Peoples R China Sun Yat Sen Univ, Guangdong Prov Key Lab Ophthalmol & Visual Sci, Guangzhou 510060, Peoples R China Sun Yat Sen Univ, Zhongshan Ophthalm Ctr, State Key Lab Ophthalmol, 54 Xianlie South Rd, Guangzhou 510060, Peoples R ChinaZhong, Guisheng论文数: 0 引用数: 0 h-index: 0机构: ShanghaiTech Univ, iHuman Inst, Shanghai 201210, Peoples R China ShanghaiTech Univ, Sch Life Sci & Technol, Shanghai 201210, Peoples R China Sun Yat Sen Univ, Zhongshan Ophthalm Ctr, State Key Lab Ophthalmol, 54 Xianlie South Rd, Guangzhou 510060, Peoples R ChinaZhou, Xiaolai论文数: 0 引用数: 0 h-index: 0机构: Sun Yat Sen Univ, Zhongshan Ophthalm Ctr, State Key Lab Ophthalmol, 54 Xianlie South Rd, Guangzhou 510060, Peoples R China Sun Yat Sen Univ, Guangdong Prov Key Lab Ophthalmol & Visual Sci, Guangzhou 510060, Peoples R China Sun Yat Sen Univ, Zhongshan Ophthalm Ctr, State Key Lab Ophthalmol, 54 Xianlie South Rd, Guangzhou 510060, Peoples R China
- [2] Novel AAV capsid variant for efficient and effective inner ear gene therapyHUMAN GENE THERAPY, 2022, 33 (23-24) : A31 - A31Rossi, A.论文数: 0 引用数: 0 h-index: 0机构: Hannover Med Sch, Hannover, Germany Hannover Med Sch, Hannover, GermanyMarx, J.论文数: 0 引用数: 0 h-index: 0机构: Hannover Med Sch, Hannover, Germany Hannover Med Sch, Hannover, GermanyHuang, P.论文数: 0 引用数: 0 h-index: 0机构: Univ Kansas, Lawrence, KS 66045 USA Hannover Med Sch, Hannover, GermanyWarnecke, A.论文数: 0 引用数: 0 h-index: 0机构: Hannover Med Sch, Hannover, Germany Hannover Med Sch, Hannover, GermanySchambach, A.论文数: 0 引用数: 0 h-index: 0机构: Hannover Med Sch, Hannover, Germany Harvard Med Sch, Boston, MA 02115 USA Hannover Med Sch, Hannover, GermanyStacker, H.论文数: 0 引用数: 0 h-index: 0机构: Univ Kansas, Lawrence, KS 66045 USA Hannover Med Sch, Hannover, GermanyBuening, H.论文数: 0 引用数: 0 h-index: 0机构: Hannover Med Sch, Hannover, Germany Hannover Med Sch, Hannover, Germany
- [3] Novel AAV Vector for Delivery of Transgenes to the Photoreceptors and RPE via Intravitreal Injection Enables Rescue of Multiple Models of Retinal DiseaseMOLECULAR THERAPY, 2020, 28 (04) : 400 - 400论文数: 引用数: h-index:机构:Mishra, Manish论文数: 0 引用数: 0 h-index: 0机构: Tufts Univ, Dev Mol & Chem Biol, Boston, MA 02111 USA Tufts Univ, Dev Mol & Chem Biol, Boston, MA 02111 USA
- [4] Novel AAV capsids for intravitreal gene therapy of photoreceptor disordersEMBO MOLECULAR MEDICINE, 2021, 13 (04)Pavlou, Marina论文数: 0 引用数: 0 h-index: 0机构: Ludwig Maximilians Univ Munchen, Dept Ophthalmol, Munich, Germany Ludwig Maximilians Univ Munchen, Dept Pharm, Ctr Integrated Prot Sci Munich, Munich, Germany Ludwig Maximilians Univ Munchen, Dept Ophthalmol, Munich, GermanySchon, Christian论文数: 0 引用数: 0 h-index: 0机构: Ludwig Maximilians Univ Munchen, Dept Pharm, Ctr Integrated Prot Sci Munich, Munich, Germany Ludwig Maximilians Univ Munchen, Dept Ophthalmol, Munich, GermanyOccelli, Laurence M.论文数: 0 引用数: 0 h-index: 0机构: Michigan State Univ, Dept Small Anim Clin Sci, E Lansing, MI 48824 USA Ludwig Maximilians Univ Munchen, Dept Ophthalmol, Munich, GermanyRossi, Axel论文数: 0 引用数: 0 h-index: 0机构: Hannover Med Sch, Inst Expt Haematol, Lab Infect Biol & Gene Transfer, Hannover, Germany Ludwig Maximilians Univ Munchen, Dept Ophthalmol, Munich, GermanyMeumann, Nadja论文数: 0 引用数: 0 h-index: 0机构: Hannover Med Sch, Inst Expt Haematol, Lab Infect Biol & Gene Transfer, Hannover, Germany Hannover Med Sch, REBIRTH Res Ctr Translat Regenerat Med, Hannover, Germany Ludwig Maximilians Univ Munchen, Dept Ophthalmol, Munich, GermanyBoyd, Ryan F.论文数: 0 引用数: 0 h-index: 0机构: Charles River Labs, Ophthalmol Serv, Mattawan, MI USA Ludwig Maximilians Univ Munchen, Dept Ophthalmol, Munich, GermanyBartoe, Joshua T.论文数: 0 引用数: 0 h-index: 0机构: Charles River Labs, Ophthalmol Serv, Mattawan, MI USA Ludwig Maximilians Univ Munchen, Dept Ophthalmol, Munich, GermanySiedlecki, Jakob论文数: 0 引用数: 0 h-index: 0机构: Ludwig Maximilians Univ Munchen, Dept Ophthalmol, Munich, Germany Ludwig Maximilians Univ Munchen, Dept Ophthalmol, Munich, GermanyGerhardt, Maximilian J.论文数: 0 引用数: 0 h-index: 0机构: Ludwig Maximilians Univ Munchen, Dept Ophthalmol, Munich, Germany Ludwig Maximilians Univ Munchen, Dept Ophthalmol, Munich, GermanyBabutzka, Sabrina论文数: 0 引用数: 0 h-index: 0机构: Ludwig Maximilians Univ Munchen, Dept Ophthalmol, Munich, Germany Ludwig Maximilians Univ Munchen, Dept Pharm, Ctr Integrated Prot Sci Munich, Munich, Germany Ludwig Maximilians Univ Munchen, Dept Ophthalmol, Munich, GermanyBogedein, Jacqueline论文数: 0 引用数: 0 h-index: 0机构: Ludwig Maximilians Univ Munchen, Dept Ophthalmol, Munich, Germany Ludwig Maximilians Univ Munchen, Dept Pharm, Ctr Integrated Prot Sci Munich, Munich, Germany Ludwig Maximilians Univ Munchen, Dept Ophthalmol, Munich, GermanyWagner, Johanna E.论文数: 0 引用数: 0 h-index: 0机构: Ludwig Maximilians Univ Munchen, Dept Pharm, Ctr Integrated Prot Sci Munich, Munich, Germany Ludwig Maximilians Univ Munchen, Dept Ophthalmol, Munich, GermanyPriglinger, Siegfried G.论文数: 0 引用数: 0 h-index: 0机构: Ludwig Maximilians Univ Munchen, Dept Ophthalmol, Munich, Germany Ludwig Maximilians Univ Munchen, Dept Ophthalmol, Munich, GermanyBiel, Martin论文数: 0 引用数: 0 h-index: 0机构: Ludwig Maximilians Univ Munchen, Dept Pharm, Ctr Integrated Prot Sci Munich, Munich, Germany Ludwig Maximilians Univ Munchen, Dept Ophthalmol, Munich, GermanyPetersen-Jones, Simon M.论文数: 0 引用数: 0 h-index: 0机构: Michigan State Univ, Dept Small Anim Clin Sci, E Lansing, MI 48824 USA Ludwig Maximilians Univ Munchen, Dept Ophthalmol, Munich, GermanyBuening, Hildegard论文数: 0 引用数: 0 h-index: 0机构: Hannover Med Sch, Inst Expt Haematol, Lab Infect Biol & Gene Transfer, Hannover, Germany Hannover Med Sch, REBIRTH Res Ctr Translat Regenerat Med, Hannover, Germany Ludwig Maximilians Univ Munchen, Dept Ophthalmol, Munich, GermanyMichalakis, Stylianos论文数: 0 引用数: 0 h-index: 0机构: Ludwig Maximilians Univ Munchen, Dept Ophthalmol, Munich, Germany Ludwig Maximilians Univ Munchen, Dept Pharm, Ctr Integrated Prot Sci Munich, Munich, Germany Ludwig Maximilians Univ Munchen, Dept Ophthalmol, Munich, Germany
- [5] A Penetrable AAV2 Capsid Variant for Efficient Intravitreal Gene Delivery to the RetinaINVESTIGATIVE OPHTHALMOLOGY & VISUAL SCIENCE, 2025, 66 (01)He, Xiaoyu论文数: 0 引用数: 0 h-index: 0机构: Shanghai Jiao Tong Univ, Sch Med, Peoples Hosp 9, Dept Ophthalmol, 639 Zhizaoju Rd, Shanghai 200011, Peoples R China Shanghai Key Lab Orbital Dis & Ocular Oncol, Shanghai, Peoples R China Shanghai Jiao Tong Univ, Sch Med, Peoples Hosp 9, Dept Ophthalmol, 639 Zhizaoju Rd, Shanghai 200011, Peoples R ChinaFu, Yidian论文数: 0 引用数: 0 h-index: 0机构: Shanghai Jiao Tong Univ, Sch Med, Peoples Hosp 9, Dept Ophthalmol, 639 Zhizaoju Rd, Shanghai 200011, Peoples R China Shanghai Key Lab Orbital Dis & Ocular Oncol, Shanghai, Peoples R China Shanghai Jiao Tong Univ, Sch Med, Peoples Hosp 9, Dept Ophthalmol, 639 Zhizaoju Rd, Shanghai 200011, Peoples R ChinaXu, Yangfan论文数: 0 引用数: 0 h-index: 0机构: Fudan Univ, Eye Ear Nose & Throat Hosp, Eye Inst, Shanghai, Peoples R China Fudan Univ, Eye Ear Nose & Throat Hosp, Dept Ophthalmol & Optometry, Shanghai, Peoples R China Shanghai Jiao Tong Univ, Sch Med, Peoples Hosp 9, Dept Ophthalmol, 639 Zhizaoju Rd, Shanghai 200011, Peoples R ChinaMa, Liang论文数: 0 引用数: 0 h-index: 0机构: Shanghai Jiao Tong Univ, Sch Med, Peoples Hosp 9, Dept Ophthalmol, 639 Zhizaoju Rd, Shanghai 200011, Peoples R China Shanghai Key Lab Orbital Dis & Ocular Oncol, Shanghai, Peoples R China Shanghai Jiao Tong Univ, Sch Med, Peoples Hosp 9, Dept Ophthalmol, 639 Zhizaoju Rd, Shanghai 200011, Peoples R ChinaChai, Peiwei论文数: 0 引用数: 0 h-index: 0机构: Shanghai Jiao Tong Univ, Sch Med, Peoples Hosp 9, Dept Ophthalmol, 639 Zhizaoju Rd, Shanghai 200011, Peoples R China Shanghai Key Lab Orbital Dis & Ocular Oncol, Shanghai, Peoples R China Shanghai Jiao Tong Univ, Sch Med, Peoples Hosp 9, Dept Ophthalmol, 639 Zhizaoju Rd, Shanghai 200011, Peoples R ChinaShi, Hanhan论文数: 0 引用数: 0 h-index: 0机构: Shanghai Jiao Tong Univ, Sch Med, Peoples Hosp 9, Dept Ophthalmol, 639 Zhizaoju Rd, Shanghai 200011, Peoples R China Shanghai Key Lab Orbital Dis & Ocular Oncol, Shanghai, Peoples R China Shanghai Jiao Tong Univ, Sch Med, Peoples Hosp 9, Dept Ophthalmol, 639 Zhizaoju Rd, Shanghai 200011, Peoples R ChinaYao, Yizheng论文数: 0 引用数: 0 h-index: 0机构: Soochow Univ, Inst Neurosci, Jiangsu Key Lab Neuropsychiat Dis, Suzhou, Peoples R China Soochow Univ, Affiliated Hosp 2, Clin Res Ctr Neurol Dis, Suzhou, Peoples R China Shanghai Jiao Tong Univ, Sch Med, Peoples Hosp 9, Dept Ophthalmol, 639 Zhizaoju Rd, Shanghai 200011, Peoples R ChinaGe, Shengfang论文数: 0 引用数: 0 h-index: 0机构: Shanghai Jiao Tong Univ, Sch Med, Peoples Hosp 9, Dept Ophthalmol, 639 Zhizaoju Rd, Shanghai 200011, Peoples R China Shanghai Key Lab Orbital Dis & Ocular Oncol, Shanghai, Peoples R China Shanghai Jiao Tong Univ, Sch Med, Peoples Hosp 9, Dept Ophthalmol, 639 Zhizaoju Rd, Shanghai 200011, Peoples R ChinaJia, Renbing论文数: 0 引用数: 0 h-index: 0机构: Shanghai Jiao Tong Univ, Sch Med, Peoples Hosp 9, Dept Ophthalmol, 639 Zhizaoju Rd, Shanghai 200011, Peoples R China Shanghai Key Lab Orbital Dis & Ocular Oncol, Shanghai, Peoples R China Shanghai Jiao Tong Univ, Sch Med, Peoples Hosp 9, Dept Ophthalmol, 639 Zhizaoju Rd, Shanghai 200011, Peoples R ChinaWen, Xuyang论文数: 0 引用数: 0 h-index: 0机构: Shanghai Jiao Tong Univ, Sch Med, Peoples Hosp 9, Dept Ophthalmol, 639 Zhizaoju Rd, Shanghai 200011, Peoples R China Shanghai Key Lab Orbital Dis & Ocular Oncol, Shanghai, Peoples R China Shanghai Jiao Tong Univ, Sch Med, Peoples Hosp 9, Dept Ophthalmol, 639 Zhizaoju Rd, Shanghai 200011, Peoples R ChinaYang, Zhi论文数: 0 引用数: 0 h-index: 0机构: Shanghai Jiao Tong Univ, Sch Med, Peoples Hosp 9, Dept Ophthalmol, 639 Zhizaoju Rd, Shanghai 200011, Peoples R China Shanghai Key Lab Orbital Dis & Ocular Oncol, Shanghai, Peoples R China Shanghai Jiao Tong Univ, Sch Med, Peoples Hosp 9, Dept Ophthalmol, 639 Zhizaoju Rd, Shanghai 200011, Peoples R ChinaFan, Xianqun论文数: 0 引用数: 0 h-index: 0机构: Shanghai Jiao Tong Univ, Sch Med, Peoples Hosp 9, Dept Ophthalmol, 639 Zhizaoju Rd, Shanghai 200011, Peoples R China Shanghai Key Lab Orbital Dis & Ocular Oncol, Shanghai, Peoples R China Shanghai Jiao Tong Univ, Sch Med, Peoples Hosp 9, Dept Ophthalmol, 639 Zhizaoju Rd, Shanghai 200011, Peoples R China
- [6] A novel dual AAV approach for intravitreal gene therapy of Stargardt diseaseHUMAN GENE THERAPY, 2022, 33 (23-24) : A26 - A26Mehlfeld, V.论文数: 0 引用数: 0 h-index: 0机构: ViGeneron GmbH, Planegg, Germany Univ Munich LMU, Munich, Germany ViGeneron GmbH, Planegg, GermanySplith, V.论文数: 0 引用数: 0 h-index: 0机构: ViGeneron GmbH, Planegg, Germany ViGeneron GmbH, Planegg, GermanyBartoschek, M.论文数: 0 引用数: 0 h-index: 0机构: ViGeneron GmbH, Planegg, Germany ViGeneron GmbH, Planegg, GermanyPandurangi, J.论文数: 0 引用数: 0 h-index: 0机构: ViGeneron GmbH, Planegg, Germany ViGeneron GmbH, Planegg, GermanyBoehm, S.论文数: 0 引用数: 0 h-index: 0机构: ViGeneron GmbH, Planegg, Germany ViGeneron GmbH, Planegg, GermanyRiedmayr, L. M.论文数: 0 引用数: 0 h-index: 0机构: Univ Munich LMU, Munich, Germany ViGeneron GmbH, Planegg, GermanyMichalakis, S.论文数: 0 引用数: 0 h-index: 0机构: Univ Munich LMU, Munich, Germany ViGeneron GmbH, Planegg, GermanyBiel, M.论文数: 0 引用数: 0 h-index: 0机构: Univ Munich LMU, Munich, Germany ViGeneron GmbH, Planegg, Germany论文数: 引用数: h-index:机构:
- [7] RPE-Directed Gene Therapy Improves Mitochondrial Function in Murine Dry AMD ModelsINTERNATIONAL JOURNAL OF MOLECULAR SCIENCES, 2023, 24 (04)Millington-Ward, Sophia论文数: 0 引用数: 0 h-index: 0机构: Trinity Coll Dublin, Smurfit Inst Genet, Sch Genet & Microbiol, Dublin D02 VF25, Ireland Trinity Coll Dublin, Smurfit Inst Genet, Sch Genet & Microbiol, Dublin D02 VF25, IrelandChadderton, Naomi论文数: 0 引用数: 0 h-index: 0机构: Trinity Coll Dublin, Smurfit Inst Genet, Sch Genet & Microbiol, Dublin D02 VF25, Ireland Trinity Coll Dublin, Smurfit Inst Genet, Sch Genet & Microbiol, Dublin D02 VF25, IrelandFinnegan, Laura K.论文数: 0 引用数: 0 h-index: 0机构: Trinity Coll Dublin, Smurfit Inst Genet, Sch Genet & Microbiol, Dublin D02 VF25, Ireland Trinity Coll Dublin, Smurfit Inst Genet, Sch Genet & Microbiol, Dublin D02 VF25, IrelandPost, Iris J. M.论文数: 0 引用数: 0 h-index: 0机构: Trinity Coll Dublin, Smurfit Inst Genet, Sch Genet & Microbiol, Dublin D02 VF25, Ireland Trinity Coll Dublin, Smurfit Inst Genet, Sch Genet & Microbiol, Dublin D02 VF25, IrelandCarrigan, Matthew论文数: 0 引用数: 0 h-index: 0机构: Trinity Coll Dublin, Smurfit Inst Genet, Sch Genet & Microbiol, Dublin D02 VF25, Ireland Trinity Coll Dublin, Smurfit Inst Genet, Sch Genet & Microbiol, Dublin D02 VF25, IrelandNixon, Rachel论文数: 0 引用数: 0 h-index: 0机构: Trinity Coll Dublin, Smurfit Inst Genet, Sch Genet & Microbiol, Dublin D02 VF25, Ireland Trinity Coll Dublin, Smurfit Inst Genet, Sch Genet & Microbiol, Dublin D02 VF25, IrelandHumphries, Marian M.论文数: 0 引用数: 0 h-index: 0机构: Trinity Coll Dublin, Smurfit Inst Genet, Sch Genet & Microbiol, Dublin D02 VF25, Ireland Trinity Coll Dublin, Smurfit Inst Genet, Sch Genet & Microbiol, Dublin D02 VF25, IrelandHumphries, Pete论文数: 0 引用数: 0 h-index: 0机构: Trinity Coll Dublin, Smurfit Inst Genet, Sch Genet & Microbiol, Dublin D02 VF25, Ireland Trinity Coll Dublin, Smurfit Inst Genet, Sch Genet & Microbiol, Dublin D02 VF25, IrelandKenna, Paul F.论文数: 0 引用数: 0 h-index: 0机构: Trinity Coll Dublin, Smurfit Inst Genet, Sch Genet & Microbiol, Dublin D02 VF25, Ireland Royal Victoria Eye & Ear Hosp, Res Fdn, Dublin D02XK51, Ireland Trinity Coll Dublin, Smurfit Inst Genet, Sch Genet & Microbiol, Dublin D02 VF25, IrelandPalfi, Arpad论文数: 0 引用数: 0 h-index: 0机构: Trinity Coll Dublin, Smurfit Inst Genet, Sch Genet & Microbiol, Dublin D02 VF25, Ireland Trinity Coll Dublin, Smurfit Inst Genet, Sch Genet & Microbiol, Dublin D02 VF25, IrelandFarrar, G. Jane论文数: 0 引用数: 0 h-index: 0机构: Trinity Coll Dublin, Smurfit Inst Genet, Sch Genet & Microbiol, Dublin D02 VF25, Ireland Trinity Coll Dublin, Smurfit Inst Genet, Sch Genet & Microbiol, Dublin D02 VF25, Ireland
- [8] AAV Vector for Delivery of Transgenes to the Photoreceptors and RPE via Intravitreal Injection or cornea via Intracameral Injection Enables Rescue of Multiple Models of Ocular DiseaseINVESTIGATIVE OPHTHALMOLOGY & VISUAL SCIENCE, 2023, 64 (08)Kumar-Singh, Rajendra论文数: 0 引用数: 0 h-index: 0机构: Tufts Univ, Dev Mol & Chem Biol, Sch Med, Boston, MA USA Tufts Univ, Dev Mol & Chem Biol, Sch Med, Boston, MA USASivalingam, Kalaiselvi论文数: 0 引用数: 0 h-index: 0机构: Tufts Univ, Dev Mol & Chem Biol, Sch Med, Boston, MA USA Tufts Univ, Dev Mol & Chem Biol, Sch Med, Boston, MA USA
- [9] Efficiency of gene therapy via intravitreal injection in primate conesINVESTIGATIVE OPHTHALMOLOGY & VISUAL SCIENCE, 2022, 63 (07)Giarmarco, Michelle M.论文数: 0 引用数: 0 h-index: 0机构: Univ Washington, Ophthalmol, Seattle, WA 98195 USA Univ Washington, Ophthalmol, Seattle, WA 98195 USA论文数: 引用数: h-index:机构:Rowlan, Jessica论文数: 0 引用数: 0 h-index: 0机构: Univ Washington, Ophthalmol, Seattle, WA 98195 USA Univ Washington, Ophthalmol, Seattle, WA 98195 USARezeanu, Dragos论文数: 0 引用数: 0 h-index: 0机构: Univ Washington, Ophthalmol, Seattle, WA 98195 USA Univ Washington, Ophthalmol, Seattle, WA 98195 USABembry, Briyana论文数: 0 引用数: 0 h-index: 0机构: Univ Washington, Ophthalmol, Seattle, WA 98195 USA Univ Washington, Ophthalmol, Seattle, WA 98195 USA论文数: 引用数: h-index:机构:论文数: 引用数: h-index:机构:Kuchenbecker, James A.论文数: 0 引用数: 0 h-index: 0机构: Univ Washington, Ophthalmol, Seattle, WA 98195 USA Univ Washington, Ophthalmol, Seattle, WA 98195 USA
- [10] Novel AAV capsid variant for muscle-directed gene therapyHUMAN GENE THERAPY, 2021, 32 (19-20) : A29 - A29Lemoine, J.论文数: 0 引用数: 0 h-index: 0机构: Univ Evry, Univ Paris Saclay, Inserm, Genethon,Integrare Res Unit UMR S951, Evry, France Univ Evry, Univ Paris Saclay, Inserm, Genethon,Integrare Res Unit UMR S951, Evry, FranceJust, S.论文数: 0 引用数: 0 h-index: 0机构: Hannover Med Sch, Inst Expt Hematol, Hannover, Germany Univ Evry, Univ Paris Saclay, Inserm, Genethon,Integrare Res Unit UMR S951, Evry, FranceDominguez, N.论文数: 0 引用数: 0 h-index: 0机构: Univ Evry, Univ Paris Saclay, Inserm, Genethon,Integrare Res Unit UMR S951, Evry, France Univ Evry, Univ Paris Saclay, Inserm, Genethon,Integrare Res Unit UMR S951, Evry, FranceGaly, A.论文数: 0 引用数: 0 h-index: 0机构: Univ Evry, Univ Paris Saclay, Inserm, Genethon,Integrare Res Unit UMR S951, Evry, France Univ Evry, Univ Paris Saclay, Inserm, Genethon,Integrare Res Unit UMR S951, Evry, FranceBuening, N.论文数: 0 引用数: 0 h-index: 0机构: Hannover Med Sch, Inst Expt Hematol, Hannover, Germany Univ Evry, Univ Paris Saclay, Inserm, Genethon,Integrare Res Unit UMR S951, Evry, FranceRichard, I.论文数: 0 引用数: 0 h-index: 0机构: Univ Evry, Univ Paris Saclay, Inserm, Genethon,Integrare Res Unit UMR S951, Evry, France Univ Evry, Univ Paris Saclay, Inserm, Genethon,Integrare Res Unit UMR S951, Evry, France