Sustained FVIII Expression with a Tolerable, Titratable, Fully Non-Viral Gene Therapy for Hemophilia a

被引：0

作者：

Schwerk, Johannes ^{[1
]}

Barajas-Mora, Mauricio ^{[1
]}

Wang, Hua ^{[1
]}

Truong, Brian ^{[1
]}

Bennett, Michael ^{[1
]}

Cam, Nicholas ^{[1
]}

Clancey, James ^{[1
]}

Davis, Alicia ^{[1
]}

Hajj, Khal ^{[1
]}

Jacques, Bonnie ^{[1
]}

Tamayo, Johnnatan ^{[1
]}

Yen, James ^{[1
]}

Rychak, Joshua ^{[1
]}

Madison, Blair ^{[1
]}

机构：

[1] Poseida Therapeut, San Diego, CA USA

来源：

BLOOD | 2024年 / 144卷

关键词：

D O I：

10.1182/blood-2024-211223

中图分类号：

R5 [内科学];

学科分类号：

1002 ; 100201 ;

摘要：

引用

页码：7462 / 7463

页数：2

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