Preliminary Safety and Efficacy of HG004 Gene Therapy Trial for Leber's Congenital Amaurosis Associated with Mutations in RPE65 Gene

被引：0
|
作者：
Fei, Ping [1 ]
Yang, Yuan [1 ]
Peng, Jie [1 ]
Zhang, Xiang [1 ]
Wang, Yanfei [2 ]
Zhang, Shuaishuai [2 ]
Yao, Xuan [2 ]
Luk, Alvin [3 ]
Yuan, Yiqun [2 ]
Zhao, Peiquan [1 ]
机构：
[1] Shanghai Jiao Tong Univ, Xinhua Hosp, Shanghai, Peoples R China
[2] Huidagene Therapeut Co Ltd, Shanghai, Peoples R China
[3] Huidagene Therapeut Inc, Clinton, NJ USA
来源：
MOLECULAR THERAPY | 2024年 / 32卷 / 04期
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D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
915
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收藏
页码：450 / 450
页数：1
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