PROGRESSION OF DISEASE BURDEN AMONG BOYS WITH DUCHENNE MUSCULAR DYSTROPHY (DMD) ACCORDING TO AMBULATORY STATUS AND AGE AT LOSS OF AMBULATION (LoA)

被引：0
|
作者：
Gordish-Dressman, H. [1 ]
Zhang, R. [2 ]
Kamstra, R. [3 ]
Werner, C. [4 ]
Liu, E. [5 ]
Morrison, K. [3 ]
Tomazos, I [5 ]
机构：
[1] Childrens Natl Hosp, Washington, DC USA
[2] PTC Therapeut Sweden AB, Stockholm, AB, Sweden
[3] Precis Analyt Inc, Montreal, PQ, Canada
[4] PTC Therapeut, Frankfurt, Germany
[5] PTC Therapeut Inc, South Plainfield, NJ USA
来源：
VALUE IN HEALTH | 2024年 / 27卷 / 06期
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中图分类号：
F [经济];
学科分类号：
02 ;
摘要：
CO120
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页码：S39 / S39
页数：1
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