Advancing gene editing by engineering miniature CRISPR-Cas Un1Cas12f1

被引:0
|
作者
Tang, Weimin [1 ,2 ]
机构
[1] Harvard Med Sch, Boston Childrens Hosp, Lab Biomat & Drug Delivery, Boston, MA 02115 USA
[2] Harvard Med Sch, Boston Childrens Hosp, Dept Med Crit Care, Boston, MA 02115 USA
来源
MOLECULAR THERAPY NUCLEIC ACIDS | 2024年 / 35卷 / 03期
关键词
D O I
10.1016/j.omtn.2024.102302
中图分类号
R-3 [医学研究方法]; R3 [基础医学];
学科分类号
1001 ;
摘要
引用
收藏
页数:2
相关论文
共 50 条
  • [31] CRISPR-Cas Activators for Engineering Gene Expression in Higher Eukaryotes
    Casas-Mollano, J. Armando
    Zinselmeier, Matthew H.
    Erickson, Samuel E.
    Smanski, Michael J.
    CRISPR JOURNAL, 2020, 3 (05): : 350 - 364
  • [32] Discovery and Engineering of a Miniature CRISPR-Cas Type V-L System
    Alfonse, Lauren E.
    Ornstein, Alexa
    Doherty, Erin
    Rachman, Jenna M.
    Sasaki, Tomoaki
    McMahon, Blake
    Wessells, Quinton
    Garrity, Anthony J.
    Munoz, Gabrielle Z.
    Maben, Zachary
    Bose, Mishti
    Yan, Paul
    Biasella, Amy
    Cheng, David R.
    DiTommaso, Tia
    Murphy, John E.
    Hoffman, Gregory R.
    MOLECULAR THERAPY, 2023, 31 (04) : 271 - 271
  • [33] SnapShot: Class 1 CRISPR-Cas Systems
    Makarova, Kira S.
    Zhang, Feng
    Koonin, Eugene V.
    CELL, 2017, 168 (05) : 946 - +
  • [34] Structure of the miniature type V-F CRISPR-Cas effector enzyme
    Takeda, Satoru N.
    Nakagawa, Ryoya
    Okazaki, Sae
    Hirano, Hisato
    Kobayashi, Kan
    Kusakizako, Tsukasa
    Nishizawa, Tomohiro
    Yamashita, Keitaro
    Nishimasu, Hiroshi
    Nureki, Osamu
    MOLECULAR CELL, 2021, 81 (03) : 558 - 570.e3
  • [35] Synergistic Engineering of CRISPR-Cas Nucleases Enables Robust Mammalian Genome Editing
    Chen, Yang-Can
    Hu, Yan-Ping
    Wang, Xin-Ge
    Luo, Sheng-Qiu
    Tian, Shin-Shay
    Zhao, Xiao-Ping
    Li, Wei
    MOLECULAR THERAPY, 2022, 30 (04) : 459 - 459
  • [36] Synergistic engineering of CRISPR-Cas nucleases enables robust mammalian genome editing
    Chen, Yangcan
    Hu, Yanping
    Wang, Xinge
    Luo, Shengqiu
    Yang, Ning
    Chen, Yi
    Li, Zhikun
    Zhou, Qi
    Li, Wei
    INNOVATION, 2022, 3 (04):
  • [37] Comprehensive assessment of miniature CRISPR-Cas12f nucleases for gene disruption
    Changchang Xin
    Jianhang Yin
    Shaopeng Yuan
    Liqiong Ou
    Mengzhu Liu
    Weiwei Zhang
    Jiazhi Hu
    Nature Communications, 13
  • [38] Comprehensive assessment of miniature CRISPR-Cas12f nucleases for gene disruption
    Xin, Changchang
    Yin, Jianhang
    Yuan, Shaopeng
    Ou, Liqiong
    Liu, Mengzhu
    Zhang, Weiwei
    Hu, Jiazhi
    NATURE COMMUNICATIONS, 2022, 13 (01)
  • [39] Viral Delivery of Compact CRISPR-Cas12f for Gene Editing Applications
    Sharrar, Allison
    Meacham, Zuriah
    Staples-Ager, Johanna
    de Tacca, Luisa Arake
    Rabuka, David
    Collingwood, Trevor
    Schelle, Michael
    CRISPR JOURNAL, 2024, 7 (03): : 150 - 155
  • [40] Molecular insights and rational engineering of a compact CRISPR-Cas effector Cas12h1 with a broad-spectrum PAM
    Zheng, Weiwei
    Li, Hongyu
    Liu, Mengxi
    Wei, Yuhang
    Liu, Bo
    Li, Zekai
    Xiong, Chenyang
    Huang, Shiqing
    Hu, Chunyi
    Ouyang, Songying
    SIGNAL TRANSDUCTION AND TARGETED THERAPY, 2025, 10 (01)