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- [41] Effectiveness of patisiran after switching from tafamidis for the treatment of hereditary transthyretin-mediated amyloidosis with polyneuropathyEUROPEAN JOURNAL OF NEUROLOGY, 2024, 31 (09)Labeyrie, Celine论文数: 0 引用数: 0 h-index: 0机构: Univ Paris Saclay, Assistance Publ Hop Paris AP HP, Ctr Hosp Univ CHU Bicetre, Neurol Dept,CERAMIC,INSERM U1195, 78,Ave Gen Leclerc, F-94270 Le Kremlin Bicetre, France Univ Paris Saclay, Assistance Publ Hop Paris AP HP, Ctr Hosp Univ CHU Bicetre, Neurol Dept,CERAMIC,INSERM U1195, 78,Ave Gen Leclerc, F-94270 Le Kremlin Bicetre, FranceMerkel, Madeline论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA USA Univ Paris Saclay, Assistance Publ Hop Paris AP HP, Ctr Hosp Univ CHU Bicetre, Neurol Dept,CERAMIC,INSERM U1195, 78,Ave Gen Leclerc, F-94270 Le Kremlin Bicetre, FranceSethi, Sakshi论文数: 0 引用数: 0 h-index: 0机构: Anal Grp, Boston, MA USA Univ Paris Saclay, Assistance Publ Hop Paris AP HP, Ctr Hosp Univ CHU Bicetre, Neurol Dept,CERAMIC,INSERM U1195, 78,Ave Gen Leclerc, F-94270 Le Kremlin Bicetre, FrancePopadic, Lyuba论文数: 0 引用数: 0 h-index: 0机构: Anal Grp, Boston, MA USA Univ Paris Saclay, Assistance Publ Hop Paris AP HP, Ctr Hosp Univ CHU Bicetre, Neurol Dept,CERAMIC,INSERM U1195, 78,Ave Gen Leclerc, F-94270 Le Kremlin Bicetre, FranceYang, Hongbo论文数: 0 引用数: 0 h-index: 0机构: Anal Grp, Boston, MA USA Univ Paris Saclay, Assistance Publ Hop Paris AP HP, Ctr Hosp Univ CHU Bicetre, Neurol Dept,CERAMIC,INSERM U1195, 78,Ave Gen Leclerc, F-94270 Le Kremlin Bicetre, FranceSweetser, Marianne T.论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA USA Univ Paris Saclay, Assistance Publ Hop Paris AP HP, Ctr Hosp Univ CHU Bicetre, Neurol Dept,CERAMIC,INSERM U1195, 78,Ave Gen Leclerc, F-94270 Le Kremlin Bicetre, FranceLin, Hollis论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA USA Univ Paris Saclay, Assistance Publ Hop Paris AP HP, Ctr Hosp Univ CHU Bicetre, Neurol Dept,CERAMIC,INSERM U1195, 78,Ave Gen Leclerc, F-94270 Le Kremlin Bicetre, FranceAdams, David论文数: 0 引用数: 0 h-index: 0机构: Univ Paris Saclay, Assistance Publ Hop Paris AP HP, Ctr Hosp Univ CHU Bicetre, Neurol Dept,CERAMIC,INSERM U1195, 78,Ave Gen Leclerc, F-94270 Le Kremlin Bicetre, France Univ Paris Saclay, Assistance Publ Hop Paris AP HP, Ctr Hosp Univ CHU Bicetre, Neurol Dept,CERAMIC,INSERM U1195, 78,Ave Gen Leclerc, F-94270 Le Kremlin Bicetre, France
- [42] Long-term Integrated Safety of Patisiran in Patients with Hereditary Transthyretin-Mediated Amyloidosis with PolyneuropathyJOURNAL OF CARDIAC FAILURE, 2020, 26 (10) : S67 - S68Gillmore, Julian论文数: 0 引用数: 0 h-index: 0机构: UCL, London, England UCL, London, England论文数: 引用数: h-index:机构:Dispenzieri, Angela论文数: 0 引用数: 0 h-index: 0机构: Mayo Clin Rochester, Rochester, MN USA UCL, London, EnglandPolydefkis, Michael论文数: 0 引用数: 0 h-index: 0机构: Johns Hopkins, Baltimore, MD USA UCL, London, EnglandGonzalez-Duarte, Alejandra论文数: 0 引用数: 0 h-index: 0机构: Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, Mexico UCL, London, EnglandSekijima, Yoshiki论文数: 0 引用数: 0 h-index: 0机构: Shinshu Univ Hosp, Matsumoto, Nagano, Japan UCL, London, EnglandSweetser, Marianne T.论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA USA UCL, London, EnglandArum, Seth论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA USA UCL, London, EnglandWang, Jing Jing论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA USA UCL, London, EnglandWhite, Matthew T.论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA USA UCL, London, EnglandMaurer, Mathew论文数: 0 引用数: 0 h-index: 0机构: Columbia Univ, New York, NY USA UCL, London, England
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- [44] Preclinical evaluation of RNAi as a treatment for transthyretin-mediated amyloidosisAMYLOID-JOURNAL OF PROTEIN FOLDING DISORDERS, 2016, 23 (02): : 109 - 118Butler, James S.论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA 02142 USA Alnylam Pharmaceut, Cambridge, MA 02142 USAChan, Amy论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA 02142 USA Alnylam Pharmaceut, Cambridge, MA 02142 USACostelha, Susete论文数: 0 引用数: 0 h-index: 0机构: Univ Porto, Inst Invest & Inovacao Saude, Rua Campo Alegre 823, P-4100 Oporto, Portugal IBMC Inst Mol & Cell Biol Porto, Mol Neurobiol, Oporto, Portugal Alnylam Pharmaceut, Cambridge, MA 02142 USAFishman, Shannon论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA 02142 USA Alnylam Pharmaceut, Cambridge, MA 02142 USAWilloughby, Jennifer L. S.论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA 02142 USA Alnylam Pharmaceut, Cambridge, MA 02142 USABorland, Todd D.论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA 02142 USA Alnylam Pharmaceut, Cambridge, MA 02142 USAMilstein, Stuart论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA 02142 USA Alnylam Pharmaceut, Cambridge, MA 02142 USAFoster, Donald J.论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA 02142 USA Alnylam Pharmaceut, Cambridge, MA 02142 USAGoncalves, Paula论文数: 0 引用数: 0 h-index: 0机构: Univ Porto, Inst Invest & Inovacao Saude, Rua Campo Alegre 823, P-4100 Oporto, Portugal IBMC Inst Mol & Cell Biol Porto, Mol Neurobiol, Oporto, Portugal Alnylam Pharmaceut, Cambridge, MA 02142 USAChen, Qingmin论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA 02142 USA Alnylam Pharmaceut, Cambridge, MA 02142 USAQin, June论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA 02142 USA Alnylam Pharmaceut, Cambridge, MA 02142 USABettencourt, Brian R.论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA 02142 USA Alnylam Pharmaceut, Cambridge, MA 02142 USASah, Dinah W.论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA 02142 USA Alnylam Pharmaceut, Cambridge, MA 02142 USAAlvarez, Rene论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA 02142 USA Alnylam Pharmaceut, Cambridge, MA 02142 USARajeev, Kallanthottathil G.论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA 02142 USA Alnylam Pharmaceut, Cambridge, MA 02142 USAManoharan, Muthiah论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA 02142 USA Alnylam Pharmaceut, Cambridge, MA 02142 USAFitzgerald, Kevin论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA 02142 USA Alnylam Pharmaceut, Cambridge, MA 02142 USAMeyers, Rachel E.论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA 02142 USA Alnylam Pharmaceut, Cambridge, MA 02142 USANochur, Saraswathy V.论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA 02142 USA Alnylam Pharmaceut, Cambridge, MA 02142 USA论文数: 引用数: h-index:机构:Zimmermann, Tracy S.论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA 02142 USA Alnylam Pharmaceut, Cambridge, MA 02142 USA
- [45] IDENTIFYING MIXED PHENOTYPE: EVALUATING THE PRESENCE OF POLYNEUROPATHY IN PATIENTS WITH HEREDITARY TRANSTHYRETIN-MEDIATED AMYLOIDOSIS WITH CARDIOMYOPATHYMUSCLE & NERVE, 2020, 62 : S107 - S107Grogan, Martha论文数: 0 引用数: 0 h-index: 0Hawkins, Philip论文数: 0 引用数: 0 h-index: 0Kristen, Arnt论文数: 0 引用数: 0 h-index: 0Berk, John论文数: 0 引用数: 0 h-index: 0Suhr, Ole B.论文数: 0 引用数: 0 h-index: 0Lin, Hollis论文数: 0 引用数: 0 h-index: 0Merkel, Madeline论文数: 0 引用数: 0 h-index: 0McManus, Anastasia论文数: 0 引用数: 0 h-index: 0Powell, Christine论文数: 0 引用数: 0 h-index: 0Vest, John论文数: 0 引用数: 0 h-index: 0Karsten, Verena论文数: 0 引用数: 0 h-index: 0Judge, Daniel论文数: 0 引用数: 0 h-index: 0
- [46] Identifying Mixed Phenotype: Evaluating the Presence of Polyneuropathy in Patients with Hereditary Transthyretin-Mediated Amyloidosis with CardiomyopathyNEUROLOGY, 2020, 94 (15)Merkel, Madeline论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA USA Alnylam Pharmaceut, Cambridge, MA USAGrogan, Martha论文数: 0 引用数: 0 h-index: 0机构: Mayo Clin, Rochester, MN USA Alnylam Pharmaceut, Cambridge, MA USAHawkins, Philip N.论文数: 0 引用数: 0 h-index: 0机构: Royal Free Hosp, NAC, London, England Alnylam Pharmaceut, Cambridge, MA USAKristen, Arnt V.论文数: 0 引用数: 0 h-index: 0机构: Heidelberg Univ Hosp, Heidelberg, Germany Alnylam Pharmaceut, Cambridge, MA USABerk, John L.论文数: 0 引用数: 0 h-index: 0机构: Boston Univ, Boston, MA 02215 USA Alnylam Pharmaceut, Cambridge, MA USASuhr, Ole B.论文数: 0 引用数: 0 h-index: 0机构: Umea Univ, Umea, Sweden Alnylam Pharmaceut, Cambridge, MA USALin, Hollis论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA USA Alnylam Pharmaceut, Cambridge, MA USAMcManus, Anastasia论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA USA Alnylam Pharmaceut, Cambridge, MA USAPowell, Christine论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA USA Alnylam Pharmaceut, Cambridge, MA USAVest, John论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA USA Alnylam Pharmaceut, Cambridge, MA USAKarsten, Verena论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA USA Alnylam Pharmaceut, Cambridge, MA USAJudge, Daniel P.论文数: 0 引用数: 0 h-index: 0机构: Med Univ South Carolina, Columbia, SC USA Alnylam Pharmaceut, Cambridge, MA USA
- [47] The Silent Period for Small Fiber Sensory Neuropathy Assessment in a Mixed Cohort of Transthyretin-Mediated AmyloidosisBIOMEDICINES, 2022, 10 (09)Cambieri, Chiara论文数: 0 引用数: 0 h-index: 0机构: Sapienza Univ Rome, Ctr Rare Neuromuscular Dis, Dept Human Neurosci, Policlin Umberto I, I-00185 Rome, Italy Sapienza Univ Rome, Ctr Rare Neuromuscular Dis, Dept Human Neurosci, Policlin Umberto I, I-00185 Rome, ItalyLibonati, Laura论文数: 0 引用数: 0 h-index: 0机构: Sapienza Univ Rome, Ctr Rare Neuromuscular Dis, Dept Human Neurosci, Policlin Umberto I, I-00185 Rome, Italy Sapienza Univ Rome, Ctr Rare Neuromuscular Dis, Dept Human Neurosci, Policlin Umberto I, I-00185 Rome, ItalyMoret, Federica论文数: 0 引用数: 0 h-index: 0机构: Sapienza Univ Rome, Ctr Rare Neuromuscular Dis, Dept Human Neurosci, Policlin Umberto I, I-00185 Rome, Italy Sapienza Univ Rome, Ctr Rare Neuromuscular Dis, Dept Human Neurosci, Policlin Umberto I, I-00185 Rome, ItalyTartaglia, Giorgio论文数: 0 引用数: 0 h-index: 0机构: Sapienza Univ Rome, Ctr Rare Neuromuscular Dis, Dept Human Neurosci, Policlin Umberto I, I-00185 Rome, Italy Sapienza Univ Rome, Ctr Rare Neuromuscular Dis, Dept Human Neurosci, Policlin Umberto I, I-00185 Rome, ItalyGaribaldi, Matteo论文数: 0 引用数: 0 h-index: 0机构: Sapienza Univ Rome, St Andrea Hosp, Neuromuscular & Rare Dis Ctr, Dept Neurosci Mental Hlth & Sensory Organs NESMOS, I-00189 Rome, Italy Sapienza Univ Rome, Ctr Rare Neuromuscular Dis, Dept Human Neurosci, Policlin Umberto I, I-00185 Rome, ItalyChimenti, Cristina论文数: 0 引用数: 0 h-index: 0机构: Sapienza Univ, Dept Cardiovasc Resp Nephrol Anesthesiol & Geriat, I-00185 Rome, Italy IRCCS Lazzaro Spallanzani, Cellular & Mol Cardiol Lab, I-00149 Rome, Italy Sapienza Univ Rome, Ctr Rare Neuromuscular Dis, Dept Human Neurosci, Policlin Umberto I, I-00185 Rome, ItalyInghilleri, Maurizio论文数: 0 引用数: 0 h-index: 0机构: Sapienza Univ Rome, Ctr Rare Neuromuscular Dis, Dept Human Neurosci, Policlin Umberto I, I-00185 Rome, Italy Sapienza Univ Rome, Ctr Rare Neuromuscular Dis, Dept Human Neurosci, Policlin Umberto I, I-00185 Rome, ItalyCeccanti, Marco论文数: 0 引用数: 0 h-index: 0机构: Sapienza Univ Rome, Ctr Rare Neuromuscular Dis, Dept Human Neurosci, Policlin Umberto I, I-00185 Rome, Italy Sapienza Univ Rome, Ctr Rare Neuromuscular Dis, Dept Human Neurosci, Policlin Umberto I, I-00185 Rome, Italy
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- [50] Efficacy and safety of vutrisiran for patients with hereditary transthyretin-mediated amyloidosis with polyneuropathy: a randomized clinical trialAMYLOID-JOURNAL OF PROTEIN FOLDING DISORDERS, 2023, 30 (01): : 18 - 26Adams, David论文数: 0 引用数: 0 h-index: 0机构: Univ Paris Saclay, CHU Bicetre, APHP, Neurol Dept, Le Kremlin Bicetre, France Univ Paris Saclay, CHU Bicetre, APHP, Neurol Dept, Le Kremlin Bicetre, FranceTournev, Ivailo L.论文数: 0 引用数: 0 h-index: 0机构: Med Univ, Univ Hosp Aleksandrovska, Dept Neurol, Clin Nervous Dis, Sofia, Bulgaria New Bulgarian Univ, Dept Cognit Sci, Sofia, Bulgaria Univ Paris Saclay, CHU Bicetre, APHP, Neurol Dept, Le Kremlin Bicetre, FranceTaylor, Mark S.论文数: 0 引用数: 0 h-index: 0机构: Univ Sydney, Dept Clin Immunol & Allergy, Westmead Hosp, Sydney, NSW, Australia Univ Sydney, Westmead Clin Sch, Sydney, NSW, Australia Univ Paris Saclay, CHU Bicetre, APHP, Neurol Dept, Le Kremlin Bicetre, FranceCoelho, Teresa论文数: 0 引用数: 0 h-index: 0机构: Ctr Hosp Univ Porto, Hosp Santo Antonio, Porto, Portugal Univ Paris Saclay, CHU Bicetre, APHP, Neurol Dept, Le Kremlin Bicetre, FrancePlante-Bordeneuve, Violaine论文数: 0 引用数: 0 h-index: 0机构: Univ Paris Est Creteil, CHU Henri Mondor, APHP, Neurol Amyloid Network, Creteil, France Univ Paris Saclay, CHU Bicetre, APHP, Neurol Dept, Le Kremlin Bicetre, FranceBerk, John L.论文数: 0 引用数: 0 h-index: 0机构: Boston Univ, Boston Med Ctr, Boston, MA USA Univ Paris Saclay, CHU Bicetre, APHP, Neurol Dept, Le Kremlin Bicetre, FranceGonzalez-Duarte, Alejandra论文数: 0 引用数: 0 h-index: 0机构: Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, Mexico Univ Paris Saclay, CHU Bicetre, APHP, Neurol Dept, Le Kremlin Bicetre, FranceGillmore, Julian D.论文数: 0 引用数: 0 h-index: 0机构: UCL, Royal Free Hosp, Natl Amyloidosis Ctr, London, England Univ Paris Saclay, CHU Bicetre, APHP, Neurol Dept, Le Kremlin Bicetre, FranceLow, Soon-Chai论文数: 0 引用数: 0 h-index: 0机构: Univ Malaya, Dept Med, Div Neurol, Med Ctr, Kuala Lumpur, Malaysia Univ Paris Saclay, CHU Bicetre, APHP, Neurol Dept, Le Kremlin Bicetre, FranceSekijima, Yoshiki论文数: 0 引用数: 0 h-index: 0机构: Shinshu Univ, Dept Med Neurol & Rheumatol, Sch Med, Matsumoto, Nagano, Japan Univ Paris Saclay, CHU Bicetre, APHP, Neurol Dept, Le Kremlin Bicetre, FranceObici, Laura论文数: 0 引用数: 0 h-index: 0机构: IRCCS Fdn Policlin San Matteo, Amyloidosis Res & Treatment Ctr, Pavia, Italy Univ Paris Saclay, CHU Bicetre, APHP, Neurol Dept, Le Kremlin Bicetre, FranceChen, Chongshu论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA USA Univ Paris Saclay, CHU Bicetre, APHP, Neurol Dept, Le Kremlin Bicetre, FranceBadri, Prajakta论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA USA Univ Paris Saclay, CHU Bicetre, APHP, Neurol Dept, Le Kremlin Bicetre, FranceArum, Seth M.论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA USA Univ Paris Saclay, CHU Bicetre, APHP, Neurol Dept, Le Kremlin Bicetre, FranceVest, John论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA USA Univ Paris Saclay, CHU Bicetre, APHP, Neurol Dept, Le Kremlin Bicetre, FrancePolydefkis, Michael论文数: 0 引用数: 0 h-index: 0机构: Johns Hopkins Univ, Sch Med, Dept Neurol, Baltimore, MD 21205 USA Univ Paris Saclay, CHU Bicetre, APHP, Neurol Dept, Le Kremlin Bicetre, France