Orchard Therapeutics Gains First US Approval for a Metachromatic Leukodystrophy Gene Therapy

被引：4
|
作者：
Philippidis, Alex [1 ]
机构：
[1] Mary Ann Liebert Inc, New Rochelle, NY 10801 USA
来源：
HUMAN GENE THERAPY | 2024年 / 35卷 / 7-8期
关键词：
D O I：
10.1089/hum.2024.29268.bfs
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
[No abstract available]
引用
收藏
页码：215 / 218
页数：4
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