Long-Term Efficacy of Migalastat on Renal Function and Outcomes in Patients with Fabry Disease (FD)

被引：0
|
作者：
Bichet, Daniel G. [1 ]
Feldt-Rasmussen, Ulla [2 ]
Giugliani, Roberto [3 ,4 ]
Hughes, Derralynn [5 ,6 ]
Krusinska, Eva [7 ]
Veleva-Rotse, Biliana O. [7 ]
机构：
[1] Univ Montreal, Hop Sacre Coeur, Dept Med, Montreal, PQ, Canada
[2] Natl Univ Hosp, Rigshosp, Dept Med Endocrinol & Metab, Copenhagen, Denmark
[3] Univ Fed Rio Grande do Sul, Dept Genet, HCPA, Med Genet Serv, Porto Alegre, RS, Brazil
[4] INAGEMP, Porto Alegre, RS, Brazil
[5] Royal Free London NHS Fdn Trust, Lysosomal Storage Disorders Unit, London, England
[6] UCL, London, England
[7] Amicus Therapeut Inc, Philadelphia, PA USA
来源：
JOURNAL OF THE AMERICAN SOCIETY OF NEPHROLOGY | 2021年 / 32卷 / 10期
关键词：
D O I：
暂无
中图分类号：
R5 [内科学]; R69 [泌尿科学（泌尿生殖系疾病）];
学科分类号：
1002 ; 100201 ;
摘要：
PO1312
引用
收藏
页码：420 / 421
页数：2
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