共 50 条
- [1] Base editing rescues hearing in miceNATURE REVIEWS DRUG DISCOVERY, 2020, 19 (07) : 443 - 443Villanueva, M. Teresa
- [2] In vivo base editing rescues progeria in miceNATURE REVIEWS DRUG DISCOVERY, 2021, 20 (02) : 98 - 98Cully, Megan
- [3] In vivo base editing rescues progeria in miceNature Reviews Drug Discovery, 2021, 20 : 98 - 98Megan Cully
- [4] In vivo base editing rescues Hutchinson–Gilford progeria syndrome in miceNature, 2021, 589 : 608 - 614Luke W. KoblanMichael R. ErdosChristopher WilsonWayne A. CabralJonathan M. LevyZheng-Mei XiongUrraca L. TavarezLindsay M. DavisonYantenew G. GeteXiaojing MaoGregory A. NewbySean P. DohertyNarisu NarisuQuanhu ShengChad KrilowCharles Y. LinLeslie B. GordonKan CaoFrancis S. CollinsJonathan D. BrownDavid R. Liu
- [5] Base editing of haematopoietic stem cells rescues sickle cell disease in miceNATURE, 2021, 595 (7866) : 295 - +Newby, Gregory A.Yen, Jonathan S.Woodard, Kaitly J.Mayuranathan, ThiyagarajLazzarotto, Cicera R.Li, YichaoSheppard-Tillman, HeatherPorter, Shaina N.Yao, YuMayberry, KalinEverette, Kelcee A.Jang, YoonjeongPodracky, Christopher J.Thaman, ElizabethLechauve, ChristopheSharma, AkshayHenderson, Jordana M.Richter, Michelle F.Zhao, Kevin T.Miller, Shannon M.Wang, TinaKoblan, Luke W.McCaffrey, Anton P.Tisdale, John F.Kalfa, Theodosia A.Pruett-Miller, Shondra M.Tsai, Shengdar Q.Weiss, Mitchell J.Liu, David R.
- [6] In vivo base editing rescues Hutchinson-Gilford progeria syndrome in miceNATURE, 2021, 589 (7843) : 608 - +Koblan, Luke W.Erdos, Michael R.Wilson, ChristopherCabral, Wayne A.Levy, Jonathan M.Xiong, Zheng-MeiTavarez, Urraca L.Davison, Lindsay M.Gete, Yantenew G.Mao, XiaojingNewby, Gregory A.Doherty, Sean P.Narisu, NarisuSheng, QuanhuKrilow, ChadLin, Charles Y.Gordon, Leslie B.Cao, KanCollins, Francis S.Brown, Jonathan D.Liu, David R.
- [7] Base editing of haematopoietic stem cells rescues sickle cell disease in miceNature, 2021, 595 : 295 - 302Gregory A. NewbyJonathan S. YenKaitly J. WoodardThiyagaraj MayuranathanCicera R. LazzarottoYichao LiHeather Sheppard-TillmanShaina N. PorterYu YaoKalin MayberryKelcee A. EveretteYoonjeong JangChristopher J. PodrackyElizabeth ThamanChristophe LechauveAkshay SharmaJordana M. HendersonMichelle F. RichterKevin T. ZhaoShannon M. MillerTina WangLuke W. KoblanAnton P. McCaffreyJohn F. TisdaleTheodosia A. KalfaShondra M. Pruett-MillerShengdar Q. TsaiMitchell J. WeissDavid R. Liu
- [8] Base editing rescues sickle cell diseaseNature Reviews Drug Discovery, 2021, 20 (7) : 508 - 508Sarah Crunkhorn
- [9] Base Editing Rescues Sickle Cell Disease in Human Hematopoietic Stem Cells and in MiceMOLECULAR THERAPY, 2021, 29 (04) : 63 - 64Yen, Jonathan S.Newby, Gregory A.Woodard, Kaitly J.Mayuranathan, ThiyagarajLazzarotto, CiceraLi, YichaoSheppard-Tillman, HeatherPorter, Shaina N.Yao, YuMayberry, KalinEverette, Kelcee A.Jang, YoonjeongPodracky, Christopher J.Thaman, ElizabethLechauve, ChristopherSharma, AkshayHenderson, Jordana M.Richter, Michelle F.Zhao, Kevin T.Miller, Shannon M.Wang, TinaKoblan, Luke W.McCaffrey, Anton P.Tisdale, John F.Kalfa, Theodosia A.Pruett-Miller, Shondra M.Tsai, Shengdar Q.Weiss, Mitchell J.Liu, David R.
- [10] In Vivo Postnatal Base Editing Restores Sensory Transduction and Transiently Rescues Hearing in a Mouse Model of Recessive DeafnessMOLECULAR THERAPY, 2020, 28 (04) : 562 - 562Yeh, Wei-HsiShubina-Oleinik, OlgaLevy, Jonathan M.Pan, BifengNewby, Gregory A.Wornow, MichaelBurt, RachelChen, Jonathan C.Holt, Jeffrey R.Liu, David R.