Patient reported outcome measures in a large cohort of patients with type 1 Gaucher disease

被引：0
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作者：
Tama Dinur
Majdolen Istaiti
Dafna Frydman
Michal Becker-Cohen
Jeff Szer
Ari Zimran
Shoshana Revel-Vilk
机构：
[1] Shaare Zedek Medical Centre,Gaucher Unit
[2] The Hebrew University of Jerusalem,Faculty of Medicine
[3] Royal Melbourne Hospital,Peter MacCallum Cancer Centre
[4] University of Melbourne,Department of Medicine
来源：
Orphanet Journal of Rare Diseases | / 15卷
关键词：
Gaucher disease; Patients reported outcome; Mobile survey; Adult patients; Quality of life;
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