A randomized double-blind, placebo-controlled trial of ganaxolone in children and adolescents with fragile X syndrome

被引：0
|
作者：
Andrew Ligsay
Anke Van Dijck
Danh V. Nguyen
Reymundo Lozano
Yanjun Chen
Erika S. Bickel
David Hessl
Andrea Schneider
Kathleen Angkustsiri
Flora Tassone
Berten Ceulemans
R. Frank Kooy
Randi J. Hagerman
机构：
[1] University of California,Medical Investigation of Neurodevelopmental Disorders (MIND) Institute
[2] Davis Medical Center,Department of Medical Genetics
[3] University of California,Department of Neurology
[4] Davis School of Medicine,Pediatric Neurology
[5] University of Antwerp,Department of Medicine
[6] University Hospital Antwerp,Biostatistics Institute for Clinical and Translational Science
[7] University of Antwerp,Seaver Autism Center for Research and Treatment, Department of Genetics and Genomic Sciences, Psychiatry, and Pediatrics
[8] University of California,Department of Pediatrics
[9] Irvine School of Medicine,Department of Psychiatry and Behavioral Sciences
[10] University of California,Department of Biochemistry and Molecular Medicine, School of Medicine
[11] Icahn School of Medicine at Mount Sinai,undefined
[12] University of California,undefined
[13] Davis Medical Center,undefined
[14] University of California,undefined
[15] Davis Medical Center,undefined
[16] University of California,undefined
来源：
Journal of Neurodevelopmental Disorders | 2017年 / 9卷
关键词：
Fragile X syndrome; Ganaxolone; Clinical trial; Children; Adolescents;
D O I：
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