Changes in PCSK 9 and apolipoprotein B100 in Niemann–Pick disease after enzyme replacement therapy with olipudase alfa

被引：0
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作者：
Bethanie Garside
Jan Hoong Ho
See Kwok
Yifen Liu
Shaishav Dhage
Rachelle Donn
Zohaib Iqbal
Simon A. Jones
Handrean Soran
机构：
[1] University of Manchester,Lipid Research Group, Division of Cardiovascular Sciences
[2] Manchester University NHS Foundation Trust,Cardiovascular Trials Unit, Manchester Royal Infirmary
[3] University of Manchester,Faculty of Biology, Medicine and Health
[4] Manchester University NHS Foundation Trust,Manchester Centre for Genomic Medicine, St Marys Hospital
来源：
Orphanet Journal of Rare Diseases | / 16卷
关键词：
Acid sphingomyelinase deficiency; Apolipoprotein B100; Proprotein convertase subtilisin/klexin type 9; Tumour necrosis factor α; Low density lipoprotein cholesterol; Enzyme replacement therapy;
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