Recommendations on hematopoietic stem cell transplantation for inherited bone marrow failure syndromes

被引：0

作者：

R Peffault de Latour

C Peters

B Gibson

B Strahm

A Lankester

C D de Heredia

D Longoni

F Fioredda

F Locatelli

I Yaniv

J Wachowiak

J Donadieu

A Lawitschka

M Bierings

M Wlodarski

S Corbacioglu

S Bonanomi

S Samarasinghe

T Leblanc

C Dufour

J-H Dalle

机构：

[1] Service d’Hématologie Greffe,Department of Pediatrics and Adolescent Medicine

[2] Hôpital Saint-Louis,Department of Pediatrics, Division of Immuno

[3] AP-HP,Hematology and Stem Cell Transplantation

[4] Stem Cell Transplantation Unit,Dipartimento di Emato Oncologia Pediatrica

[5] St Anna Children’s Hospital,Dipartimento di Onco

[6] Royal Hospital for Sick Children,Ematologia Pediatrica e Medicina Trasfusionale

[7] Pediatric Hematology and Oncology,Pediatric Hematology Oncology and Stem Cell Transplantation Division

[8] University Medical Centre,Department of Pediatric Oncology

[9] Leiden University Medical Centre,Department of Pediatrics

[10] Servicio de Oncología y Hematología Pediátricas,undefined

[11] Hospital Vall d’Hebron,undefined

[12] Bone Marrow Transplantation Unit,undefined

[13] San Gerardo Hospital,undefined

[14] Ematologia Clinica e di Laboratorio,undefined

[15] IRCCS Istituto G. Gaslini,undefined

[16] U.O. di Oncologia Pediatrica,undefined

[17] IRCCS Ospedale Pediatrico Bambino Gesù,undefined

[18] Schneider Children's Medical Centre of Israel,undefined

[19] Sackler Faculty of Medicine Tel Aviv University,undefined

[20] Hematology and Transplantology,undefined

[21] University of Medical Sciences,undefined

[22] Service d'Hémato-Oncologie Pédiatrique,undefined

[23] Hopital Trousseau AP-HP,undefined

[24] Paris Registre des neutropénies,undefined

[25] Centre de référence des déficits immunitaires héréditaires (neutropénies),undefined

[26] BMT-Unit,undefined

[27] University Medical Centre Utrecht Pediatrics,undefined

[28] Hematology and Oncology,undefined

[29] University of Freiburg,undefined

[30] Pediatric Hematology,undefined

[31] Oncology and Stem Cell Transplantation,undefined

[32] Children's Hospital,undefined

[33] University of Regensburg,undefined

[34] Pediatric Hematology Unit,undefined

[35] San Gerardo Hospital,undefined

[36] Pediatric Hematology,undefined

[37] Great Ormond Street Hospital,undefined

[38] Service d’hémato-immunologie pédiatrique,undefined

[39] GH Robert-Debré,undefined

[40] AP-HP,undefined

[41] Pediatric Hematology,undefined

[42] G. Gaslini Institute,undefined

[43] Université Paris Diderot—Paris 7,undefined

[44] Pres Paris-Cité Sorbonne,undefined

来源：

Bone Marrow Transplantation | 2015年 / 50卷

关键词：

D O I：

暂无

中图分类号：

学科分类号：

摘要：

Allogeneic hematopoietic stem cell transplantation (HSCT) offers the potential to cure patients with an inherited bone marrow failure syndrome (IBMFS). However, the procedure involves the risk of treatment-related mortality and may be associated with significant early and late morbidity. For these reasons, the benefits should be carefully weighed against the risks. IBMFS are rare, whereas case reports and small series in the literature illustrate highly heterogeneous practices in terms of indications for HSCT, timing, stem cell source and conditioning regimens. A consensus meeting was therefore held in Vienna in September 2012 on behalf of the European Group for Blood and Marrow Transplantation to discuss HSCT in the setting of IBMFS. This report summarizes the recommendations from this expert panel, including indications for HSCT, timing, stem cell source and conditioning regimen.

引用

页码：1168 / 1172

页数：4

共 50 条

[1] Recommendations on hematopoietic stem cell transplantation for inherited bone marrow failure syndromes
de Latour, R. Peffault
Peters, C.
Gibsons, B.
Strahm, B.
Lankester, A.
de Heredia, C. D.
Longoni, D.
Fioredda, F.
Locatelli, F.
Yaniv, I.
Wachowiak, J.
Donadieu, J.
Lawitschka, A.
Bierings, M.
Wlodarski, M.
Corbacioglu, S.
Bonanomi, S.
Samarasinghe, S.
Leblanc, T.
Dufour, C.
Dalle, J-H
[J]. BONE MARROW TRANSPLANTATION, 2015, 50 (09) : 1168 - 1172
[2] Allogeneic hematopoietic stem cell transplantation for inherited bone marrow failure syndromes
Jean-Hugues Dalle
Régis Peffault de Latour
[J]. International Journal of Hematology, 2016, 103 : 373 - 379
[3] Allogeneic hematopoietic stem cell transplantation for inherited bone marrow failure syndromes
Dalle, Jean-Hugues
de latour, Regis Peffault
[J]. INTERNATIONAL JOURNAL OF HEMATOLOGY, 2016, 103 (04) : 373 - 379
[4] HEMATOPOIETIC CELL TRANSPLANTATION FOR INHERITED BONE MARROW FAILURE SYNDROMES
Narita, Atsushi
[J]. PEDIATRIC BLOOD & CANCER, 2024, 71 : S7 - S7
[5] Hematopoietic stem cell transplantation for classical inherited bone marrow failure syndromes: an update
Pierri, Filomena
Faraci, Maura
Giardino, Stefano
Dufour, Carlo
[J]. EXPERT REVIEW OF HEMATOLOGY, 2021, 14 (10) : 911 - 925
[6] HEMATOPOIETIC STEM CELL TRANSPLANTATION IN INHERITED BONE MARROW FAILURE SYNDROMES - EXPERIENCE OF A SINGLE CENTRE
Vieira, Claudia
Teixeira, Alexandra
Campilho, Fernando
Vaz, Carlos Pinho
Ferreira, Rosa
Almeida, Marta
Ferreira, Ana
Roncon, Susana
Carvalhais, Alzira
Norton, Lucilia
Campos, Antonio
[J]. PEDIATRIC BLOOD & CANCER, 2009, 53 (05) : 840 - 840
[7] Recent advances in hematopoietic cell transplantation for inherited bone marrow failure syndromes
Sakaguchi, Hirotoshi
Yoshida, Nao
[J]. INTERNATIONAL JOURNAL OF HEMATOLOGY, 2022, 116 (01) : 16 - 27
[8] Recent advances in hematopoietic cell transplantation for inherited bone marrow failure syndromes
Hirotoshi Sakaguchi
Nao Yoshida
[J]. International Journal of Hematology, 2022, 116 : 16 - 27
[9] Disease-specific hematopoietic stem cell transplantation in children with inherited bone marrow failure syndromes
Li, Qian
Luo, Changying
Luo, Chengjuan
Wang, Jianmin
Li, Benshang
Ding, Lixia
Chen, Jing
[J]. ANNALS OF HEMATOLOGY, 2017, 96 (08) : 1389 - 1397
[10] Disease-specific hematopoietic stem cell transplantation in children with inherited bone marrow failure syndromes
Qian Li
Changying Luo
Chengjuan Luo
Jianmin Wang
Benshang Li
Lixia Ding
Jing Chen
[J]. Annals of Hematology, 2017, 96 : 1389 - 1397

← 1 2 3 4 5 →