Preferential expression of SCN1A in GABAergic neurons improves survival and epileptic phenotype in a mouse model of Dravet syndrome

被引：0
|
作者：
Ana Ricobaraza
Maria Bunuales
Manuela Gonzalez-Aparicio
Saja Fadila
Moran Rubinstein
Irene Vides-Urrestarazu
Julliana Banderas
Noemi Sola-Sevilla
Rocio Sanchez-Carpintero
Jose Luis Lanciego
Elvira Roda
Adriana Honrubia
Patricia Arnaiz
Ruben Hernandez-Alcoceba
机构：
[1] CIMA,Gene Therapy and Regulation of Gene Expression Program
[2] University of Navarra,Sackler Faculty of Medicine
[3] CIMA,Department of Human Molecular Genetics and Biochemistry, Sackler Faculty of Medicine
[4] Goldschleger Eye Research Institute,University Clinic of Navarra, Dravet Syndrome Unit, Pediatric Neurology Unit, IdiSNA
[5] Tel Aviv University,Department of Neuroscience
[6] Tel Aviv University,undefined
[7] Sagol School of Neuroscience,undefined
[8] Tel Aviv University,undefined
[9] Navarra Institute for Health Research,undefined
[10] CIMA,undefined
[11] University of Navarra,undefined
[12] Instituto de Investigación Sanitaria de Navarra (IdiSNA),undefined
[13] Centro de Investigación Biomédica en Red de Enfermedades Neurodegenerativas (CiberNed),undefined
来源：
Journal of Molecular Medicine | 2023年 / 101卷
关键词：
Nav1.1; Dravet syndrome; Epileptic encephalopathy; Adenoviral vector; ErbB4; GABAergic neuron; DP3V;
D O I：
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中图分类号：
学科分类号：
摘要：
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页码：1587 / 1601
页数：14
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