Limitations in a frataxin knockdown cell model for Friedreich ataxia in a high-throughput drug screen

被引：0
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作者：
Nadège Calmels
Hervé Seznec
Pascal Villa
Laurence Reutenauer
Marcel Hibert
Jacques Haiech
Pierre Rustin
Michel Koenig
Hélène Puccio
机构：
[1] CNRS/INSERM/Université Louis Pasteur,IGBMC (Institut de Génétique et de Biologie Moléculaire et Cellulaire)
[2] ESBS Pôle API,IFR 85/PCBIS (Plateforme de Chimie Biologique Intégrative de Strasbourg)
[3] UMR7175/CNRS/Université Louis Pasteur,Interface Physique Biologie, Centre d'Etudes Nucléaires de Bordeaux
[4] INSERM U676,Gradignan
[5] Hôpital Robert Debré,undefined
[6] CNRS/IN2P3-UMR5797,undefined
来源：
BMC Neurology | / 9卷
关键词：
Friedreich Ataxia; FRDA Patient; Recessive Ataxia; Frataxin Protein; Frataxin Level;
D O I：
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