Improving clinical trial design for Duchenne muscular dystrophy

被引：0
|
作者：
Luciano Merlini
Patrizia Sabatelli
机构：
[1] Istituto Ortopedico Rizzoli,Laboratory of Musculoskeletal Cell Biology
[2] IRCCS,undefined
[3] CNR National Research Council of Italy,undefined
[4] Institute of Molecular Genetics,undefined
来源：
BMC Neurology | / 15卷
关键词：
Duchenne muscular dystrophy; Dystrophin evaluation; Clinical trial; Corticosteroid treatment; Exon skipping; Splice modulation;
D O I：
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