The experience of a charity in translating the results of basic research to therapies for patients

被引：0
|
作者：
Lucia Monaco
机构：
[1] Fondazione Telethon,
来源：
Orphanet Journal of Rare Diseases | / 9卷 / Suppl 1期
关键词：
Gene Therapy; Leukodystrophy; Metachromatic Leukodystrophy; Trial Office; Improve Life Quality;
D O I：
10.1186/1750-1172-9-S1-O20
中图分类号：
学科分类号：
摘要：
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