Patient and family experience with transthyretin amyloid cardiomyopathy (ATTR-CM) and polyneuropathy (ATTR-PN) amyloidosis: results of two focus groups

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作者：
David Rintell
Dena Heath
Florencia Braga Mendendez
Elizabeth Cross
Theodore Cross
Vincent Knobel
Bruno Gagnon
Cameron Turtle
Alan Cohen
Edward Kalmykov
Jonathan Fox
机构：
[1] BridgeBio,
[2] Amyloidosis Research Consortium,undefined
[3] Alianza Argentina de Pacientes,undefined
[4] Cross Associates,undefined
[5] Eidos Therapeutics,undefined
来源：
Orphanet Journal of Rare Diseases | / 16卷
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