CRISPR gene-editing therapies for hypertrophic cardiomyopathy

被引：5
|
作者：
Alanna Strong
机构：
[1] Children’s Hospital of Philadelphia, Division of Human Genetics
[2] Children’s Hospital of Philadelphia, The Center for Applied Genomics
[3] Perelman School of Medicine,Department of Pediatrics
[4] University of Pennsylvania,undefined
来源：
Nature Medicine | 2023年 / 29卷 / 2期
关键词：
D O I：
10.1038/s41591-022-02184-5
中图分类号：
学科分类号：
摘要：
Pre-symptomatic gene editing in preclinical models of hypertrophic cardiomyopathy shows therapeutic promise; clinical studies are now needed to assess safety and efficacy in humans.
引用
收藏
页码：305 / 306
页数：1
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