MINIGENE DESIGNS FOR PRE-CLINICAL STUDIES IN THE ULTRA-RARE SBF1/MTMR5-RELATED NEUROPATHY

被引：0

|

作者：

Ramsoomair, Christian ^{[1
]}

Danzi, Matt ^{[1
]}

Medina, Jessica ^{[1
]}

Isom, Daniel ^{[1
]}

Rebelo, Adriana ^{[1
]}

Jacobs, Elizabeth ^{[1
]}

Saporta, Mario ^{[2
]}

Dohrn, Maike ^{[1
]}

Zuchner, Stephan ^{[1
]}

机构：

[1] Univ Miami, Miller Sch Med, Miami, FL USA

[2] Univ Miami, Miller Sch Med, Dept Neurol, Miami, FL USA

来源：

JOURNAL OF THE PERIPHERAL NERVOUS SYSTEM | 2022年 / 27卷

关键词：

Charcot-Marie-Tooth disease; CMT; gene therapy; minigene; neuropathy;

D O I：

暂无

中图分类号：

R74 [神经病学与精神病学];

学科分类号：

摘要：

引用

收藏

页码：S113 / S113

页数：1

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