Second Generation AAV-Mediated Gene Therapy to Mitigate Risk for Alzheimer's Disease in APOE4/4Homozygotes

被引:0
|
作者
Montel, Rachel A. [1 ]
Frenk, Esther [1 ]
Crystal, Ronald G. [1 ]
Stiles, Katie M. [1 ]
机构
[1] Weill Cornell Med, Dept Genet Med, New York, NY USA
关键词
D O I
暂无
中图分类号
Q81 [生物工程学(生物技术)]; Q93 [微生物学];
学科分类号
071005 ; 0836 ; 090102 ; 100705 ;
摘要
838
引用
收藏
页码:395 / 395
页数:1
相关论文
共 50 条
  • [1] Second Generation APOE2+APOE4- AAV-Mediated Gene Therapy for APOE Homozygotes at Risk for Alzheimer's Disease
    Montel, Rachel
    Frenk, Esther
    Crystal, Ronald G.
    Stiles, Katie M.
    [J]. MOLECULAR THERAPY, 2021, 29 (04) : 167 - 168
  • [2] AAV-Mediated APOE Gene Silencing for Alzheimer's Disease
    Hentschel, Lisa
    Oudshoorn-Dickmann, Maroeska
    Wattimury, Hendrina
    Boggiani, Lorenzo
    Moreno, Fiona
    Tripathi, Shrijana
    Pereira, Ines Lopes
    Nogueira, Ana
    Peris, Sara Gimeno
    Villamil, Javier
    Spronck, Lisa
    Bosma, Bas
    Kusuma, Angga
    Dobrynin, Greg
    Liu, Ying Poi
    [J]. MOLECULAR THERAPY, 2022, 30 (04) : 433 - 434
  • [4] ApoE4: A RISK FACTOR FOR ALZHEIMER'S DISEASE
    Agarwala, A.
    Durakoglugil, M.
    Xian, D.
    Bowen, I
    Herz, J.
    [J]. JOURNAL OF INVESTIGATIVE MEDICINE, 2011, 59 (02) : 469 - 469
  • [5] THE ALZHEIMER'S PREVENTION INITIATIVE GENERATION STUDY: A PRECLINICAL TRIAL IN APOE4 HOMOZYGOTES
    Tariot, P. N.
    Langbaum, J.
    Reiman, E.
    Graf, A.
    Lopez, C. Lopez
    Ryan, M.
    [J]. GERONTOLOGIST, 2016, 56 : 626 - 627
  • [6] The Alzheimer's Prevention Initiative Generation Study: A Preclinical Trial in APOE4 Homozygotes
    Tariot, Pierre
    Langbaum, Jessica
    Schneider, Lon
    Thomas, Ronald G.
    Graf, Ana
    Lopez-Lopez, Cristina
    Caputo, Angelika
    Lenz, Robert
    Vargas, Gabriel
    Reiman, Eric M.
    [J]. NEUROPSYCHOPHARMACOLOGY, 2016, 41 : S139 - S139
  • [7] Gene therapy in APOE4 homozygote Alzheimer's disease - interim data
    Kaplitt, M.
    Leopold, P.
    Noch, E.
    Ivanidze, J.
    Chazen, J. L.
    Crystal, R.
    Kaminsky, S.
    Bowe, H.
    Wang, M.
    Ballon, D.
    Dyke, J.
    Sondhi, D.
    Gandy, S.
    Giannantoni-Ibelli, G.
    Reha, A.
    Renukuntla, V.
    Barth, J. A.
    [J]. HUMAN GENE THERAPY, 2022, 33 (23-24) : A12 - A13
  • [8] Development of ApoE4 targeted therapy of Alzheimer's disease
    Michaelson, D. M.
    Luz, I
    Liraz, O.
    Boehm, A.
    Smorodinsky, N., I
    [J]. JOURNAL OF MOLECULAR NEUROSCIENCE, 2013, 51 : S81 - S81
  • [9] APOE4 testing for Alzheimer's disease
    Karlawish, JHT
    Sachs, GA
    [J]. JOURNAL OF THE AMERICAN GERIATRICS SOCIETY, 1997, 45 (09) : 1153 - 1154
  • [10] Olfactory Dysfunction in ApoE ε4/4 Homozygotes with Alzheimer's Disease
    Oleson, Stephanie
    Murphy, Claire
    [J]. JOURNAL OF ALZHEIMERS DISEASE, 2015, 46 (03) : 791 - 803