Long-term agalsidase beta therapy is associated with improvements in pain and quality of life among patients with Fabry disease

被引:0
|
作者
Guffon, N.
Germain, D. P.
Waldek, S.
Banikazemi, M.
Bushinsky, D. A.
Charrow, J.
Lee, P.
Loew, T.
Vedder, A. C.
Wilcox, W. R.
机构
[1] Hop Edouard Herriot, Lyon, France
[2] Hop Europeen Georges Pompidou, Paris, France
[3] Hope Hosp, Manchester, Lancs, England
[4] Mt Sinai Sch Med, New York, NY USA
[5] Univ Rochester, Sch Med, Rochester, NY 14627 USA
[6] Childrens Mem Hosp, Chicago, IL 60614 USA
[7] UCL Natl Hosp Neurol & Neurosurg, London WC1N 3BG, England
[8] Univ Iowa Hosp & Clin, Iowa City, IA 52242 USA
[9] Univ Amsterdam, Acad Med Ctr, NL-1105 AZ Amsterdam, Netherlands
[10] Cedars Sinai Med Ctr, Los Angeles, CA 90048 USA
关键词
D O I
10.1016/S0149-2918(07)80154-8
中图分类号
R9 [药学];
学科分类号
1007 ;
摘要
引用
收藏
页码:S31 / S31
页数:1
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