Innovations Needed for Effective Implementation of Ex Vivo Gene Therapies

被引：1
|
作者：
Cavazzana, Marina [1 ,2 ,3 ,4 ]
机构：
[1] Necker Childrens Hosp, AP HP, Biotherapy Dept, Paris, France
[2] Grp Hosp Univ Ouest, AP HP, Biotherapy Clin Invest Ctr, INSERM, Paris, France
[3] Paris Descartes Sorbonne Paris Cite Univ, Imagine Inst, Paris, France
[4] INSERM, UMR 1163, Lab Human Lymphohematopoiesis, Paris, France
来源：
FRONTIERS IN MEDICINE | 2017年 / 4卷
基金：
欧盟地平线“2020”;
关键词：
gene therapy; hematopoietic stem progenitor cells; genome-editing technology; dyserythropoiesis; hemoglobinopathies; Wiskott-Aldrich syndrome; THALASSEMIA;
D O I：
10.3389/fmed.2017.00029
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
[No abstract available]
引用
收藏
页数：3
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